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Review

Non-transfusion-dependent thalassemia and thalassemia intermedia: epidemiology, complications, and management

Pages 191-204 | Accepted 15 Oct 2015, Published online: 25 Nov 2015

Keep up to date with the latest research on this topic with citation updates for this article.

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Wenqian Zhang, Xiaoqiang Han, Jie Deng, Rui Zhou, Xiaoyun Du, Cheng Wu & Mingqun Li. (2023) Two Novel α-Thalassemia Mutations CD 39 -C [Thr > Pro] and CD 109 ACC > CCC [Thr > Pro] Identified in Two Chinese Families: A Case Report. Hemoglobin 47:4, pages 172-179.
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John Porter, Ali Taher, Vip Viprakasit, Antonis Kattamis, Thomas D Coates, Maciej Garbowski, Franz Dürrenberger, Vania Manolova, Frank Richard & M. Domenica Cappellini. (2021) Oral ferroportin inhibitor vamifeport for improving iron homeostasis and erythropoiesis in β-thalassemia: current evidence and future clinical development. Expert Review of Hematology 14:7, pages 633-644.
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Yunchen Luo, Rekha Bajoria, Yongrong Lai, Hongfei Pan, Qiaochuan Li, Zhongming Zhang, Pijian Yang, Ratna Chatterjee & Yuzhen Liang. (2019) Prevalence of abnormal glucose homeostasis in Chinese patients with non-transfusion-dependent thalassemia. Diabetes, Metabolic Syndrome and Obesity 12, pages 457-468.
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YunShuan Li, Quan Ren, Yali Zhou, Pingping Li, Wanhua Lin & Xiaolin Yin. (2018) Thalidomide has a significant effect in patients with thalassemia intermedia. Hematology 23:1, pages 50-54.
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Naouel Ben Salah, Rayan Bou-Fakhredin, Fethi Mellouli & Ali T. Taher. (2017) Revisiting beta thalassemia intermedia: past, present, and future prospects. Hematology 22:10, pages 607-616.
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Racha Halawi, Irene Motta, Ali Taher & Maria Domenica Cappellini. (2016) Deferasirox: an orphan drug for chronic iron overload in non-transfusion dependent thalassemia syndromes. Expert Opinion on Orphan Drugs 4:6, pages 677-686.
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Syahirah Amnani Suhaimi, Ihsan Nazurah Zulkipli, Hazim Ghani & Mas Rina Wati Abdul-Hamid. (2022) Applications of next generation sequencing in the screening and diagnosis of thalassemia: A mini-review. Frontiers in Pediatrics 10.
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