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Prospects for antisense peptide nucleic acid (PNA) therapies for HIV

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Pages 975-989 | Published online: 17 Jun 2009

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Roberto Gambari. (2014) Peptide nucleic acids: a review on recent patents and technology transfer. Expert Opinion on Therapeutic Patents 24:3, pages 267-294.
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Hongchao Zheng, Victor Clausse, Harsha Amarasekara, Sharlyn J. Mazur, Istvan Botos & Daniel H. Appella. (2023) Variation of Tetrahydrofurans in Thyclotides Enhances Oligonucleotide Binding and Cellular Uptake of Peptide Nucleic Acids. JACS Au 3:7, pages 1952-1964.
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Bruno Mattia Bizzarri, Angelica Fanelli, Stefania Ciprini, Alessandra Giorgi, Marta De Angelis, Raoul Fioravanti, Lucia Nencioni & Raffaele Saladino. (2022) Multicomponent Synthesis of Diaminopurine and Guanine PNA’s Analogues Active against Influenza A Virus from Prebiotic Compounds. ACS Omega.
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Xingguo Liang, Mengqin Liu & Makoto Komiyama. (2021) Recognition of Target Site in Various Forms of DNA and RNA by Peptide Nucleic Acid (PNA): From Fundamentals to Practical Applications. Bulletin of the Chemical Society of Japan 94:6, pages 1737-1756.
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Jessica Gasparello, Chiara Papi, Matteo Zurlo, Roberto Corradini, Roberto Gambari & Alessia Finotti. (2019) Demonstrating specificity of bioactive peptide nucleic acids (PNAs) targeting microRNAs for practical laboratory classes of applied biochemistry and pharmacology. PLOS ONE 14:9, pages e0221923.
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Roberta Milani, Eleonora Brognara, Enrica Fabbri, Alex Manicardi, Roberto Corradini, Alessia Finotti, Jessica Gasparello, Monica Borgatti, Lucia Cosenza, Ilaria Lampronti, Maria Dechecchi, Giulio Cabrini & Roberto Gambari. (2019) Targeting miR‑155‑5p and miR‑221‑3p by peptide nucleic acids induces caspase‑3 activation and apoptosis in temozolomide‑resistant T98G glioma cells. International Journal of Oncology.
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Hongchao Zheng, Mrinmoy Saha & Daniel H. Appella. (2018) Synthesis of Fmoc-Protected ( S , S )- trans -Cyclopentane Diamine Monomers Enables the Preparation and Study of Conformationally Restricted Peptide Nucleic Acids . Organic Letters 20:23, pages 7637-7640.
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Marcin Równicki, Tomasz Pieńko, Jakub Czarnecki, Monika Kolanowska, Dariusz Bartosik & Joanna Trylska. (2018) Artificial Activation of Escherichia coli mazEF and hipBA Toxin–Antitoxin Systems by Antisense Peptide Nucleic Acids as an Antibacterial Strategy. Frontiers in Microbiology 9.
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Jianbin Wang & Michael C. Holmes. (2016) Engineering hematopoietic stem cells toward a functional cure of human immunodeficiency virus infection. Cytotherapy 18:11, pages 1370-1381.
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Eleonora Brognara, Enrica Fabbri, Giulia Montagner, Jessica Gasparello, Alex Manicardi, Roberto Corradini, Nicoletta Bianchi, Alessia Finotti, Giulia Breveglieri, Monica Borgatti, Ilaria Lampronti, Roberta Milani, Maria Dechecchi, Giulio Cabrini & Roberto Gambari. (2015) High levels of apoptosis are induced in human glioma cell lines by co-administration of peptide nucleic acids targeting miR-221 and miR-222. International Journal of Oncology.
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Dijie Liu, Ethan R. Balkin, Fang Jia, Varyanna C. Ruthengael, C. Jeffrey Smith & Michael R. Lewis. (2015) Targeted antisense radiotherapy and dose fractionation using a 177Lu-labeled anti-bcl-2 peptide nucleic acid-peptide conjugate. Nuclear Medicine and Biology 42:9, pages 704-710.
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Martínez-Montiel Nancy, Rosas-Murrieta Nora & Martínez-Contreras Rebeca. (2015) Peptidic tools applied to redirect alternative splicing events. Peptides 67, pages 1-11.
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Carlos T. Nieto, Mateo M. Salgado, Sara H. Domínguez, David Díez & Narciso M. Garrido. (2014) Rapid access with diversity to enantiopure flexible PNA monomers following asymmetric orthogonal strategies. Tetrahedron: Asymmetry 25:13-14, pages 1046-1060.
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Eleonora Brognara, Enrica Fabbri, Elena Bazzoli, Giulia Montagner, Claudio Ghimenton, Albino Eccher, Cinzia Cantù, Alex Manicardi, Nicoletta Bianchi, Alessia Finotti, Giulia Breveglieri, Monica Borgatti, Roberto Corradini, Valentino Bezzerri, Giulio Cabrini & Roberto Gambari. (2014) Uptake by human glioma cell lines and biological effects of a peptide-nucleic acids targeting miR-221. Journal of Neuro-Oncology 118:1, pages 19-28.
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Elisse C. Browne, Steven J. Langford & Belinda M. Abbott. (2013) Synthesis and effects of conjugated tocopherol analogues on peptide nucleic acid hybridisation. Organic & Biomolecular Chemistry 11:39, pages 6744.
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Indrajit Das, Jérôme Désiré, Dinesh Manvar, Isabelle Baussanne, Virendra N. Pandey & Jean-Luc Décout. (2012) A Peptide Nucleic Acid–Aminosugar Conjugate Targeting Transactivation Response Element of HIV-1 RNA Genome Shows a High Bioavailability in Human Cells and Strongly Inhibits Tat-Mediated Transactivation of HIV-1 Transcription. Journal of Medicinal Chemistry 55:13, pages 6021-6032.
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Gregory Upert, Audrey Di Giorgio, Alok Upadhyay, Dinesh Manvar, Nootan Pandey, Virendra N. Pandey & Nadia Patino. (2012) Inhibition of HIV Replication by Cyclic and Hairpin PNAs Targeting the HIV-1 TAR RNA Loop. Journal of Nucleic Acids 2012, pages 1-9.
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Peter Järver, Thibault Coursindel, Samir EL Andaloussi, Caroline Godfrey, Matthew JA Wood & Michael J Gait. (2012) Peptide-mediated Cell and In Vivo Delivery of Antisense Oligonucleotides and siRNA. Molecular Therapy - Nucleic Acids 1, pages e27.
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Enrica Fabbri, Eleonora Brognara, Monica Borgatti, Ilaria Lampronti, Alessia Finotti, Nicoletta Bianchi, Stefano Sforza, Tullia Tedeschi, Alex Manicardi, Rosangela Marchelli, Roberto Corradini & Roberto Gambari. (2011) miRNA therapeutics: delivery and biological activity of peptide nucleic acids targeting miRNAs. Epigenomics 3:6, pages 733-745.
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Jasbir Singh, Harmeet Kaur, Aditi Kaushik & Sapna Peer. (2011) A Review of Antisense Therapeutic Interventions for Molecular Biological Targets in Various Diseases. International Journal of Pharmacology 7:3, pages 294-315.
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M. Terêsa Machini Miranda, Cleber W. Liria & Cesar Remuzgo. 2010. Amino Acids, Peptides and Proteins in Organic Chemistry. Amino Acids, Peptides and Proteins in Organic Chemistry 549 569 .
Filbert Totsingan, Vipul Jain, W. Clay Bracken, Andrea Faccini, Tullia Tedeschi, Rosangela Marchelli, Roberto Corradini, Neville R. Kallenbach & Mark M. Green. (2010) Conformational Heterogeneity in PNA:PNA Duplexes. Macromolecules 43:6, pages 2692-2703.
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