Advanced search
Publication Cover
Expert Opinion on Orphan Drugs Volume 2, 2014 - Issue 11: Rare Diseases - Detection, Treatment, Care and Research
Submit an article Journal homepage
390
Views
2
CrossRef citations to date
0
Altmetric
Reviews

The emergence of gene therapy for rare diseases

M Ian PhillipsKeck Graduate Institute of Applied Life Sciences, Center for Rare Disease Therapies, 535 Watson Drive, Claremont, CA 91711, [email protected]
&
Andrew B BurnsKeck Graduate Institute of Applied Life Sciences, Center for Rare Disease Therapies, 535 Watson Drive, Claremont, CA 91711, [email protected]
Pages 1197-1209 | Published online: 28 Oct 2014

Citations (2)

Keep up to date with the latest research on this topic with citation updates for this article.

Subscribe to citation updates

Read on this site (1)

Eva Richard, Belén Pérez, Celia Pérez-Cerdá & Lourdes R Desviat. (2015) Understanding molecular mechanisms in propionic acidemia and investigated therapeutic strategies. Expert Opinion on Orphan Drugs 3:12, pages 1427-1438.
Read now

Articles from other publishers (1)

Oksana Polesskaya, Ancha Baranova, Sarah Bui, Nikolai Kondratev, Evgeniya Kananykhina, Olga Nazarenko, Tatyana Shapiro, Frances Barg Nardia, Vladimir Kornienko, Vikas Chandhoke, Istvan Stadler, Raymond Lanzafame & Max Myakishev-Rempel. (2018) Optogenetic regulation of transcription. BMC Neuroscience 19:S1.
Crossref

Reprints and Corporate Permissions

Please note: Selecting permissions does not provide access to the full text of the article, please see our help page How do I view content?

To request a reprint or corporate permissions for this article, please click on the relevant link below:

Order Reprints Request Corporate Permissions

Academic Permissions

Please note: Selecting permissions does not provide access to the full text of the article, please see our help page How do I view content?

Obtain permissions instantly via Rightslink by clicking on the button below:

Request Academic Permissions

If you are unable to obtain permissions via Rightslink, please complete and submit this Permissions form. For more information, please visit our Permissions help page.

Related research

People also read lists articles that other readers of this article have read.

Recommended articles lists articles that we recommend and is powered by our AI driven recommendation engine.

Cited by lists all citing articles based on Crossref citations.
Articles with the Crossref icon will open in a new tab.