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Bijay Dhungel, Aparna Jayachandran, Christopher J. Layton & Jason C. Steel. (2017) Seek and destroy: targeted adeno-associated viruses for gene delivery to hepatocellular carcinoma. Drug Delivery 24:1, pages 289-299.
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Read now
Articles from other publishers (23)
Ali Rajabi Zangi, Ala Amiri, Pouya Pazooki, Fatemeh Soltanmohammadi, Hamed Hamishehkar & Yousef Javadzadeh. (2023) Non-viral and viral delivery systems for hemophilia A therapy: recent development and prospects. Annals of Hematology.
Crossref
Crossref
Takafumi Hiramoto, Yuji Kashiwakura, Morisada Hayakawa, Nemekhbayar Baatartsogt, Nobuhiko Kamoshita, Tomoyuki Abe, Hiroshi Inaba, Hiroshi Nishimasu, Hideki Uosaki, Yutaka Hanazono, Osamu Nureki & Tsukasa Ohmori. (2023) PAM-flexible Cas9-mediated base editing of a hemophilia B mutation in induced pluripotent stem cells. Communications Medicine 3:1.
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Cedric Hermans, Yves Gruel, Laurent Frenzel & Evelien Krumb. (2023) How to translate and implement the current science of gene therapy into haemophilia care?. Therapeutic Advances in Hematology 14, pages 204062072211456.
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Patrizia Tornabene, Rita Ferla, Manel Llado-Santaeularia, Miriam Centrulo, Margherita Dell’Anno, Federica Esposito, Elena Marrocco, Emanuela Pone, Renato Minopoli, Carolina Iodice, Edoardo Nusco, Settimio Rossi, Hristiana Lyubenova, Anna Manfredi, Lucio Di Filippo, Antonella Iuliano, Annalaura Torella, Giulio Piluso, Francesco Musacchia, Enrico Maria Surace, Davide Cacchiarelli, Vincenzo Nigro & Alberto Auricchio. (2022) Therapeutic homology-independent targeted integration in retina and liver. Nature Communications 13:1.
Crossref
Crossref
Kenneth Lundstrom. 2022. The Biological Role of a Virus. The Biological Role of a Virus
285
341
.
Preeti Kanikarla Marie, Natalie W. Fowlkes, Vahid Afshar-Kharghan, Stephanie L. Martch, Alexey Sorokin, John Paul Shen, Van K. Morris, Arvind Dasari, Nancy You, Anil K. Sood, Michael J. Overman, Scott Kopetz & David George Menter. (2021) The Provocative Roles of Platelets in Liver Disease and Cancer. Frontiers in Oncology 11.
Crossref
Crossref
Stacy E. Croteau, Michael Wang & Allison P. Wheeler. (2020)
2021
clinical trials update: Innovations in hemophilia therapy
. American Journal of Hematology 96:1, pages 128-144.
Crossref
Crossref
Namrata Chaudhari, Amanda M. Rickard, Suki Roy, Peter Dröge & Harshyaa Makhija. (2020) A non-viral genome editing platform for site-specific insertion of large transgenes. Stem Cell Research & Therapy 11:1.
Crossref
Crossref
Benjamin J. Samelson-Jones, Jonathan D. Finn, Patricia Favaro, J. Fraser Wright & Valder R. Arruda. (2020) Timing of Intensive Immunosuppression Impacts Risk of Transgene Antibodies after AAV Gene Therapy in Nonhuman Primates. Molecular Therapy - Methods & Clinical Development 17, pages 1129-1138.
Crossref
Crossref
Kandace L. Gollomp, Bhavya S. Doshi & Valder R. Arruda. (2019) Gene therapy for hemophilia: Progress to date and challenges moving forward. Transfusion and Apheresis Science 58:5, pages 602-612.
Crossref
Crossref
Benjamin J. Samelson-Jones & Valder R. Arruda. (2019) Protein-Engineered Coagulation Factors for Hemophilia Gene Therapy. Molecular Therapy - Methods & Clinical Development 12, pages 184-201.
Crossref
Crossref
Arunachalam Muthuraman, Seema Mehdi & Narahari Rishitha. 2019. Nanoparticles in Pharmacotherapy. Nanoparticles in Pharmacotherapy
73
112
.
Donna M. DiMichele. (2018) Navigating Speed Bumps on the Innovation Highway in Hemophilia Therapeutics. HemaSphere 2:5, pages e144.
Crossref
Crossref
Rahul Bhardwaj, Goutam Rath & Amit K. Goyal. (2018) Advancement in the treatment of haemophilia. International Journal of Biological Macromolecules 118, pages 289-295.
Crossref
Crossref
Pauline Balkaransingh & Guy Young. (2017) Novel therapies and current clinical progress in hemophilia A. Therapeutic Advances in Hematology 9:2, pages 49-61.
Crossref
Crossref
Steven W. Pipe. (2018) Gene therapy for hemophilia. Pediatric Blood & Cancer 65:2, pages e26865.
Crossref
Crossref
Valder R. Arruda, Bhavya S. Doshi & Benjamin J. Samelson-Jones. (2018) Emerging therapies for hemophilia: controversies and unanswered questions. F1000Research 7, pages 489.
Crossref
Crossref
Valder R. Arruda, Bhavya S. DoshiBenjamin J. Samelson-Jones. (2017) Novel approaches to hemophilia therapy: successes and challenges. Blood 130:21, pages 2251-2256.
Crossref
Crossref
Arthur W. Nienhuis, Amit C. Nathwani & Andrew M. Davidoff. (2017) Gene Therapy for Hemophilia. Molecular Therapy 25:5, pages 1163-1167.
Crossref
Crossref
Jan Hartmann & Stacy E. Croteau. (2016) 2017 Clinical trials update: Innovations in hemophilia therapy. American Journal of Hematology 91:12, pages 1252-1260.
Crossref
Crossref
Li Zhang. (2016) Personalized medicine and blood disorders. Personalized Medicine 13:6, pages 587-596.
Crossref
Crossref
Joshua I. Siner, Benjamin J. Samelson-Jones, Julie M. Crudele, Robert A. French, Benjamin J. Lee, Shanzhen Zhou, Elizabeth Merricks, Robin Raymer, Timothy C. Nichols, Rodney M. Camire & Valder R. Arruda. (2016) Circumventing furin enhances factor VIII biological activity and ameliorates bleeding phenotypes in hemophilia models. JCI Insight 1:16.
Crossref
Crossref
V.R. Arruda & B.J. Samelson‐Jones. (2016) Gene therapy for immune tolerance induction in hemophilia with inhibitors. Journal of Thrombosis and Haemostasis 14:6, pages 1121-1134.
Crossref
Crossref