Is orphan drug pricing blowing a bubble? The unique situation of orphan drugs and why high prices will likely persist

Figures & data

Table 1. The 10 most expensive orphan drugs sold in the United States.

Drug name	Cost per Patient/per year($)	Indication
Soliris	409,500	Proxysmal Nocturnal Hemoglobinuria
Elaprase	375,000	Hunter syndrome
Naglazyme	365,000	Maroteaux–Lamy syndrome
Cinryze	350,000	Hereditary angioedema
Myozyme	300,000	Pompe disease
Gattex	295,000	Short-bowel syndrome
Arcalyst	250,000	Familial cold autoinflammatory syndrome & Muckle–Wells syndrome
Fabrazyme	200,000	Fabry disease
Cerezyme	200,000	Gaucher's disease
Aldurazyme	200,000	Hurler syndrome

Herper M [20].

Herper M. The world's most expensive drugs. Forbes. 2010. Available from: http://www.forbes.com/2010/02/19/expensive-drugs-cost-business-healthcare-rare-diseases_slide.html

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