Acknowledgements
We thank the patients who have made this work possible.
Disclosure statement
MIFJO received consultancy fees from Alnylam, Pfizer and Johnson & Johnson paid to the University Medical Centre Utrecht, outside the current work. CK has received consultancy fees, speakers fees from Alnylam and Pfizer as well as research support from AstraZeneca paid to the Maastricht University Medical Centre. ATR is a consultant for Tenaya Therapeutics. All other authors have no conflict of interest.