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Expert Review of Hematology Volume 6, 2013 - Issue 3
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Perspective

Combining gene therapy and fetal hemoglobin induction for treatment of β-thalassemia

Laura Breda Department of Pediatrics, Division of Hematology–Oncology, Weill Cornell Medical College, New York, NY, USA. [email protected]; Department of Pediatrics, Division of Hematology–Oncology, Weill Cornell Medical College, New York, NY, USA. [email protected]
,
Stefano Rivella Department of Pediatrics, Division of Hematology–Oncology, Weill Cornell Medical College, New York, NY, USA. [email protected]; Department of Cell & Development Biology, Weill Cornell Medical College, New York, NY, USA; Department of Pediatrics, Division of Hematology–Oncology, Weill Cornell Medical College, New York, NY, USA. [email protected]; Department of Cell & Development Biology, Weill Cornell Medical College, New York, NY, USA
,
Cristina Zuccato Department of Life Sciences & Biotechnology, University of Ferrara, Ferrara, Italy; Department of Life Sciences & Biotechnology, University of Ferrara, Ferrara, Italy
&
Roberto Gambari Department of Life Sciences & Biotechnology, University of Ferrara, Ferrara, Italy; Laboratory for the Development of Gene and Pharmacogenomic Therapy of Thalassaemia, Biotechnology Centre of Ferrara University, Ferrara, Italy; Department of Life Sciences & Biotechnology, University of Ferrara, Ferrara, Italy; Laboratory for the Development of Gene and Pharmacogenomic Therapy of Thalassaemia, Biotechnology Centre of Ferrara University, Ferrara, Italy
Pages 255-264 | Published online: 10 Jan 2014

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