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The American Journal of Bioethics Volume 20, 2020 - Issue 4
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CASE REPORT

Ethical Drug Development for Rare Childhood Diseases: When There Are Limited But Promising Data in Adults, How to Choose Between Safety or Efficacy Studies?

Liza-Marie JohnsonSt. Jude Children's Research Hospital; ORCID Iconhttp://orcid.org/0000-0002-7124-979XView further author information
ORCID Icon,
Devan M. DuenasSeattle Children's Research Institute; Correspondence[email protected]
ORCID Iconhttp://orcid.org/0000-0003-1630-1417View further author information
ORCID Icon &
Benjamin S. WilfondSeattle Children's Research Institute; ;University of Washington School of MedicineView further author information
Pages 111-113 | Published online: 24 Mar 2020
 
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DISCLOSURE STATEMENT

Liza-Marie Johnson and Benjamin S. Wilfond are the coeditors and Devan M. Duenas is the managing editor. This case was contributed by Anne Stevens.

Additional information

Funding

The challenging cases in research ethics series is supported by the Institute of Translational Health Sciences [UL1 TROO2319] with a CTSA award from the National Center for Advancing Translational Research.

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