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Cristina Martinez-Fernandez de la Camara, Jasmina Cehajic-Kapetanovic & Robert E. MacLaren. (2022) Emerging gene therapy products for RPGR-associated X-linked retinitis pigmentosa. Expert Opinion on Emerging Drugs 27:4, pages 431-443.
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Xiufang Pan, Yongping Yue, Maria Boftsi, Lakmini P. Wasala, Ngoc Tam Tran, Keqing Zhang, David J. Pintel, Phillip W. L. Tai & Dongsheng Duan. (2021) Rational engineering of a functional CpG-free ITR for AAV gene therapy. Gene Therapy 29:6, pages 333-345.
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Andrea Sodi, Sandro Banfi, Francesco Testa, Michele Della Corte, Ilaria Passerini, Elisabetta Pelo, Settimio Rossi & Francesca Simonelli. (2021) RPE65-associated inherited retinal diseases: consensus recommendations for eligibility to gene therapy. Orphanet Journal of Rare Diseases 16:1.
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Ivana Trapani, Patrizia Tornabene & Alberto Auricchio. (2020) Large gene delivery to the retina with AAV vectors: are we there yet?. Gene Therapy 28:5, pages 220-222.
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Ashley E. Neiweem, Thomas A. Ciulla & Seenu M. Hariprasad. (2021) Genetic Testing Prevalence, Guidelines, and Pitfalls in Large, University-Based Medical Systems. Ophthalmic Surgery, Lasers and Imaging Retina 52:1, pages 6-10.
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Thomas Ciulla, Mark E. Pennesi, Szilárd Kiss & Emmett T. Cunningham. (2021) DNA- and RNA-based Gene Therapies in Ophthalmology. International Ophthalmology Clinics 61:3, pages 3-16.
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