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Review

Pharmacological therapeutics in Friedreich ataxia: the present state

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Pages 895-907 | Received 17 May 2017, Accepted 14 Jul 2017, Published online: 26 Jul 2017

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David R Lynch, Kim Schadt, Elizabeth Kichula, Shana McCormack & Kimberly Y Lin. (2021) Friedreich Ataxia: Multidisciplinary Clinical Care. Journal of Multidisciplinary Healthcare 14, pages 1645-1658.
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Layne N Rodden & David R Lynch. (2021) Designing phase II clinical trials in Friedreich ataxia. Expert Opinion on Emerging Drugs 26:4, pages 415-423.
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Shaila D Ghanekar, Wai Wai Miller, Colin J Meyer, Kevin J Fenelon, Alvin Lacdao & Theresa A Zesiewicz. (2019) Orphan Drugs In Development For The Treatment Of Friedreich’s Ataxia: Focus On Omaveloxolone. Degenerative Neurological and Neuromuscular Disease 9, pages 103-107.
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Alexandra Clay, Patrick Hearle, Kim Schadt & David R. Lynch. (2019) New developments in pharmacotherapy for Friedreich ataxia. Expert Opinion on Pharmacotherapy 20:15, pages 1855-1867.
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Christian Rummey, Elizabeth Kichula & David R. Lynch. (2018) Clinical trial design for Friedreich ataxia - Where are we now and what do we need?. Expert Opinion on Orphan Drugs 6:3, pages 219-230.
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