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Review

Self-administered C1 esterase inhibitor concentrates for the management of hereditary angioedema: usability and patient acceptance

Pages 1727-1737 | Published online: 07 Sep 2016

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Marcus Maurer, Markus Magerl, Stephen Betschel, Werner Aberer, Ignacio J. Ansotegui, Emel Aygören‐Pürsün, Aleena Banerji, Noémi‐Anna Bara, Isabelle Boccon‐Gibod, Konrad Bork, Laurence Bouillet, Henrik Balle Boysen, Nicholas Brodszki, Paula J. Busse, Anette Bygum, Teresa Caballero, Mauro Cancian, Anthony Castaldo, Danny M. Cohn, Dorottya Csuka, Henriette Farkas, Mark Gompels, Richard Gower, Anete S. Grumach, Guillermo Guidos‐Fogelbach, Michihiro Hide, Hye‐Ryun Kang, Allen Phillip Kaplan, Constance Katelaris, Sorena Kiani‐Alikhan, Wei‐Te Lei, Richard Lockey, Hilary Longhurst, William R. Lumry, Andrew MacGinnitie, Alejandro Malbran, Inmaculada Martinez Saguer, Juan José Matta, Alexander Nast, Dinh Nguyen, Sandra A. Nieto‐Martinez, Ruby Pawankar, Jonathan Peter, Grzegorz Porebski, Nieves Prior, Avner Reshef, Marc Riedl, Bruce Ritchie, Farrukh Rafique Sheikh, William B. Smith, Peter J. Spaeth, Marcin Stobiecki, Elias Toubi, Lilian Agnes Varga, Karsten Weller, Andrea Zanichelli, Yuxiang Zhi, Bruce Zuraw & Timothy Craig. (2022) The international WAO/EAACI guideline for the management of hereditary angioedema—The 2021 revision and update. Allergy 77:7, pages 1961-1990.
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Marcus Maurer, Markus Magerl, Stephen Betschel, Werner Aberer, Ignacio J. Ansotegui, Emel Aygören-Pürsün, Aleena Banerji, Noémi-Anna Bara, Isabelle Boccon-Gibod, Konrad Bork, Laurence Bouillet, Henrik Balle Boysen, Nicholas Brodszki, Paula J. Busse, Anette Bygum, Teresa Caballero, Mauro Cancian, Anthony J. Castaldo, Danny M. Cohn, Dorottya Csuka, Henriette Farkas, Mark Gompels, Richard Gower, Anete S. Grumach, Guillermo Guidos-Fogelbach, Michihiro Hide, Hye-Ryun Kang, Allen P. Kaplan, Constance H. Katelaris, Sorena Kiani-Alikhan, Wei-Te Lei, Richard F. Lockey, Hilary Longhurst, William Lumry, Andrew MacGinnitie, Alejandro Malbran, Inmaculada Martinez Saguer, Juan José Matta Campos, Alexander Nast, Dinh Nguyen, Sandra A. Nieto-Martinez, Ruby Pawankar, Jonathan Peter, Grzegorz Porebski, Nieves Prior, Avner Reshef, Marc Riedl, Bruce Ritchie, Farrukh Rafique Sheikh, William B. Smith, Peter J. Spaeth, Marcin Stobiecki, Elias Toubi, Lilian Agnes Varga, Karsten Weller, Andrea Zanichelli, Yuxiang Zhi, Bruce Zuraw & Timothy Craig. (2022) The international WAO/EAACI guideline for the management of hereditary angioedema – The 2021 revision and update. World Allergy Organization Journal 15:3, pages 100627.
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Kristin Epland, Melanie Wayne & Heather Pein. (2021) Hereditary Angioedema Management: Individualization. The Journal for Nurse Practitioners 17:10, pages 1199-1203.
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Katharina Gerling, Sabrina Ölschläger, Meltem Avci-Adali, Bernd Neumann, Ernst Schweizer, Christian Schlensak, Hans-Peter Wendel & Sandra Stoppelkamp. (2020) A Novel C1-Esterase Inhibitor Oxygenator Coating Prevents FXII Activation in Human Blood. Biomolecules 10:7, pages 1042.
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Jonathan A. Bernstein, Christopher Tyson, Anurag Relan, Philippe Adams & Raf Magar. (2020) Modeling Cost-Effectiveness of On-Demand Treatment for Hereditary Angioedema Attacks. Journal of Managed Care & Specialty Pharmacy 26:2, pages 203-210.
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H. Henry Li, Marc Riedl & Jay Kashkin. (2018) Update on the Use of C1-Esterase Inhibitor Replacement Therapy in the Acute and Prophylactic Treatment of Hereditary Angioedema. Clinical Reviews in Allergy & Immunology 56:2, pages 207-218.
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Elyse Murphy, Christine Donahue, Laurel Omert, Stephanie Persons, Thomas J. Tyma, Joseph Chiao & William Lumry. (2019) Training patients for self-administration of a new subcutaneous C1-inhibitor concentrate for hereditary angioedema. Nursing Open 6:1, pages 126-135.
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Andrea Zanichelli, Giulia Maria Azin, Federico Cristina, Romualdo Vacchini & Teresa Caballero. (2018) Safety, effectiveness, and impact on quality of life of self-administration with plasma-derived nanofiltered C1 inhibitor (Berinert®) in patients with hereditary angioedema: the SABHA study. Orphanet Journal of Rare Diseases 13:1.
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Dipti Pawaskar, Michael A. Tortorici, Bruce Zuraw, Timothy Craig, Marco Cicardi, Hilary Longhurst, H. Henry Li, William R. Lumry, Inmaculada Martinez-Saguer, Joshua Jacobs, Jonathan A. Bernstein, Marc A. Riedl, Constance H. Katelaris, Paul K. Keith, Annette Feussner & Jagdev Sidhu. (2018) Population pharmacokinetics of subcutaneous C1-inhibitor for prevention of attacks in patients with hereditary angioedema. Clinical & Experimental Allergy 48:10, pages 1325-1332.
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M. Maurer, M. Magerl, I. Ansotegui, E. Aygören-Pürsün, S. Betschel, K. Bork, T. Bowen, H. Balle Boysen, H. Farkas, A. S. Grumach, M. Hide, C. Katelaris, R. Lockey, H. Longhurst, W. R. Lumry, I. Martinez-Saguer, D. Moldovan, A. Nast, R. Pawankar, P. Potter, M. Riedl, B. Ritchie, L. Rosenwasser, M. Sánchez-Borges, Y. Zhi, B. Zuraw & T. Craig. (2018) The international WAO/EAACI guideline for the management of hereditary angioedema-The 2017 revision and update. Allergy 73:8, pages 1575-1596.
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Marcus Maurer, Markus Magerl, Ignacio Ansotegui, Emel Aygören-Pürsün, Stephen Betschel, Konrad Bork, Tom Bowen, Henrik Balle Boysen, Henriette Farkas, Anete S. Grumach, Michihiro Hide, Constance Katelaris, Richard Lockey, Hilary Longhurst, William R. Lumry, Inmaculada Martinez-Saguer, Dumitru Moldovan, Alexander Nast, Ruby Pawankar, Paul Potter, Marc Riedl, Bruce Ritchie, Lanny Rosenwasser, Mario Sánchez-Borges, Yuxiang Zhi, Bruce Zuraw & Timothy Craig. (2018) The international WAO/EAACI guideline for the management of hereditary angioedema – the 2017 revision and update. World Allergy Organization Journal 11, pages 5.
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Marc A. Riedl, Jonathan A. Bernstein, Timothy Craig, Aleena Banerji, Markus Magerl, Marco Cicardi, Hilary J. Longhurst, Mustafa M. Shennak, William H. Yang, Jennifer Schranz, Jovanna Baptista & Paula J. Busse. (2017) An open-label study to evaluate the long-term safety and efficacy of lanadelumab for prevention of attacks in hereditary angioedema: design of the HELP study extension. Clinical and Translational Allergy 7:1.
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