Upsala Journal of Medical Sciences
Volume 117, 2012 - Issue 1
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Original Article
Substrate reduction therapy with miglustat for type 1 Gaucher disease: A retrospective analysis from a single institution
Maciej MachaczkaDivision of Hematology, Department of Medicine at Huddinge, Karolinska Institutet, and Hematology Center Karolinska,
Karolinska University Hospital Huddinge, Stockholm, SwedenCorrespondence[email protected]
, Robert HastDepartment of Medicine at Solna,
Karolinska Institutet, Stockholm, Sweden
, Ingrid Dahlman
Department of Endocrinology, Karolinska University Hospital Huddinge,
Stockholm, Sweden
, Richard LernerDivision of Hematology, Department of Medicine at Huddinge, Karolinska Institutet, and Hematology Center Karolinska,
Karolinska University Hospital Huddinge, Stockholm, Sweden
, Monika KlimkowskaDepartment of Clinical Pathology and Cytology,
Karolinska University Hospital Huddinge, Stockholm, Sweden
, Martin EngvallCentre for Inherited Metabolic Diseases, Karolinska University Hospital Huddinge,
Stockholm, Sweden
& Hans HägglundDivision of Hematology, Department of Medicine at Huddinge, Karolinska Institutet, and Hematology Center Karolinska,
Karolinska University Hospital Huddinge, Stockholm, Sweden
show all
Pages 28-34
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Received 30 Aug 2011, Accepted 10 Nov 2011, Published online: 17 Jan 2012
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