Open access
6,675
Views
81
CrossRef citations to date
0
Altmetric
Original Article
Preclinical evaluation of RNAi as a treatment for transthyretin-mediated amyloidosis
James S. ButlerAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Amy ChanAlnylam Pharmaceuticals, Cambridge, MA, USA, Correspondence[email protected]
, Susete CostelhaInstituto de Investigação e Inovação em Saúde, Universidade do Porto, Porto, Portugal, ;Molecular Neurobiology, IBMC – Institute for Molecular and Cell Biology Porto, Porto, PortugalCorrespondence[email protected]
, Shannon FishmanAlnylam Pharmaceuticals, Cambridge, MA, USA, Correspondence[email protected]
, Jennifer L. S. WilloughbyAlnylam Pharmaceuticals, Cambridge, MA, USA, Correspondence[email protected]
, Todd D. BorlandAlnylam Pharmaceuticals, Cambridge, MA, USA, Correspondence[email protected]
, Stuart MilsteinAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Donald J. FosterAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Paula GonçalvesInstituto de Investigação e Inovação em Saúde, Universidade do Porto, Porto, Portugal, ;Molecular Neurobiology, IBMC – Institute for Molecular and Cell Biology Porto, Porto, Portugal
, Qingmin ChenAlnylam Pharmaceuticals, Cambridge, MA, USA,
, June QinAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Brian R. BettencourtAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Dinah W. SahAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Rene AlvarezAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Kallanthottathil G. RajeevAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Muthiah ManoharanAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Kevin FitzgeraldAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Rachel E. MeyersAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Saraswathy V. NochurAlnylam Pharmaceuticals, Cambridge, MA, USA,
, Maria J. SaraivaInstituto de Investigação e Inovação em Saúde, Universidade do Porto, Porto, Portugal, ;Molecular Neurobiology, IBMC – Institute for Molecular and Cell Biology Porto, Porto, Portugal
& Tracy S. ZimmermannAlnylam Pharmaceuticals, Cambridge, MA, USA,
show all
Pages 109-118
|
Received 12 Nov 2015, Accepted 29 Feb 2016, Published online: 31 Mar 2016
Related research
People also read lists articles that other readers of this article have read.
Recommended articles lists articles that we recommend and is powered by our AI driven recommendation engine.
Cited by lists all citing articles based on Crossref citations.
Articles with the Crossref icon will open in a new tab.