1,136
Views
7
CrossRef citations to date
0
Altmetric
LETTERS TO THE EDITOR: MEDICAL ONCOLOGY

Sirolimus monotherapy for Erdheim–Chester disease

, , , , &

References

  • Haroche J, Arnaud L, Cohen-Aubart F, et al. Erdheim-Chester disease. Curr Rheumatol Rep. 2014;16:412.
  • Estrada-Veras JI, O’Brien KJ, Boyd LC, et al. The clinical spectrum of Erdheim-Chester disease: an observational cohort study. Blood Adv. 2017;1:357–366.
  • Hervier B, Arnaud L, Charlotte F, et al. Treatment of Erdheim-Chester disease with long-term high-dose interferon-α. Semin Arthritis Rheum. 2012;41:907–913.
  • Arnaud L, Hervier B, N´eel A, et al. CNS involvement and treatment with interferon-α are independent prognostic factors in Erdheim Chester disease: a multicenter survival analysis of 53 patients. Blood. 2011;117:2778–2782.
  • Haroche J, Amoura Z, Trad SG, et al. Vaiability I the efficacy of interferon-α in Erdheim-Chester disease by patient and site of involvement. Arthritis Rheum. 2006;54:3330–3336.
  • Haroche J, Charlotte F, Arnaud L, et al. High prevalence of BRAF V600E mutations in Erdheim-Chester disease but not in other non-Langerhans cell histiocytoses. Blood. 2012;120:2700–2703.
  • Haroche J, Cohen-Aubart F, Emile JF, et al. Reproducible and sustained efficacy of targeted therapy with vemurafenib in patients with BRAF(V600E)-mutated Erdheim-Chester disease. Jco. 2015;33:411–418.
  • Diamond EL, Subbiah V, Lockhart AC, et al. Vemurafenib for BRAF V600-mutant Erdheim-Chester disease and langerhans cell histiocytosis: analysis of data from the histology-independent, phase 2, open-label VE-BASKET study. JAMA Oncol. 2018;4:384–388.
  • Vaglio A, Diamond EL. Erdheim-Chester disease: the "targeted" revolution (editorial). Blood. 2017;130:1282–1284.
  • Powell JD, Pollizzi KN, Heikamp EB, et al. Regulation of immune responses by mTOR. Annu Rev Immunol. 2012;30:39–68.
  • Yuan R, Kay A, Berg WJ, et al. Targeting tumorigenesis: development and use of mTOR inhibitors in cancer therapy. J Hematol Oncol. 2009;2:45.
  • Perl A. Activation of mTOR (mechanistic target of rapamycin) in rheumatic diseases. Nat Rev Rheumatol. 2016;12:169–182.
  • McCormack FX, Inoue Y, Moss J, National Institutes of Health Rare Lung DiseasesConsortium; MILES Trial Group, et al. Efficacy and safety of sirolimus in lymphangioleiomyomatosis. N Engl J Med. 2011;364:1595–1606.
  • Gianfreda D, Nicastro M, Galetti M, et al. Sirolimus plus prednisone for Erdheim-Chester disease: an open-label trial. Blood. 2015;126:1163–1171.
  • Haroche J, Amoura Z. mTOR: a new target in Erdheim-Chester disease?. Blood. 2015;126:1151–1152.
  • Goyal G, Shah MV, Call TG, et al. Efficacy of biological agents in the treatment of Erdheim-Chester disease. Br J Haematol. 2018;183:520–524.
  • Graziani G, Podestà MA, Cucchiari D, et al. Erdheim-Chester disease: from palliative care to targeted treatment. Clin Kidney J. 2014;7:339–343.
  • Ventura-Aguiar P, Campistol JM, Diekmann F. Safety of mTOR inhibitors in adult solid organ transplantation. Exp Opin Drug Saf. 2016;15:303–319.
  • Sadowski K, Kotulska K, Jóźwiak S. Management of side effects of mTOR inhibitors in tuberous sclerosis patients. Pharmacol Rep. 2016;68:536–542.
  • Kaplan B, Qazi Y, Wellen JR. Strategies for the management of adverse events associated with mTOR inhibitors. Transplant Rev (Orlando). 2014;28:126–133.
  • Hillel AT, Gelbard A. Unleashing rapamycin in fibrosis (editorial). Oncotarget. 2015;6:15722–15723.
  • Luo L, Zhang C, Zhao J, et al. Effects of rapamycin on reduction of peridural fibrosis: an experimental study. Med Sci Monit. 2015;21:482–488.
  • Wang B, Ding W, Zhang M, et al. Rapamycin attenuates aldosterone-induced tubulointerstitial inflammation and fibrosis. Cell Physiol Biochem. 2015;35:116–125.
  • Emile JF, Diamond EL, H´elias-Rodzewicz Z, et al. Recurrent RAS and PIK3CA mutations in Erdheim-Chester disease. Blood. 2014;124:3016–3019.

Reprints and Corporate Permissions

Please note: Selecting permissions does not provide access to the full text of the article, please see our help page How do I view content?

To request a reprint or corporate permissions for this article, please click on the relevant link below:

Academic Permissions

Please note: Selecting permissions does not provide access to the full text of the article, please see our help page How do I view content?

Obtain permissions instantly via Rightslink by clicking on the button below:

If you are unable to obtain permissions via Rightslink, please complete and submit this Permissions form. For more information, please visit our Permissions help page.