113
Views
1
CrossRef citations to date
0
Altmetric
Original Articles

Five Interval Estimators of the Risk Difference Under Stratified Randomized Clinical Trials with Noncompliance and Repeated Measurements

&
Pages 756-773 | Received 08 Aug 2011, Accepted 01 Dec 2011, Published online: 20 Jun 2013

REFERENCES

  • Angrist , J. D. , Imbens , G. W. , Rubin , D. B. ( 1996 ). Identification of causal effects using instrumental variables . Journal of the American Statistical Association 91 : 444 – 456 .
  • Bernhard , G. , Compagnone , D. ( 1989 ). Binary data in prerandomized designs . Biometrical Journal 31 : 29 – 33 .
  • Casella , G. , Berger , R. L. ( 1990 ). Statistical Inference . Belmont , CA : Duxbury .
  • Cochran , W. G. ( 1977 ). Sampling Techniques . New York , NY : Wiley .
  • Edwardes , M. D. ( 1995 ). A confidence interval for Pr(X < Y) – Pr(X > Y) estimated from simple cluster samples . Biometrics 51 : 571 – 578 .
  • Fleiss , J. L. ( 1981 ). Statistical Methods for Rates and Proportions. , 2nd ed. New York , NY : Wiley .
  • Fleiss , J. L. ( 1986 ). The Design and Analysis of Clinical Experiments . New York , NY : Wiley .
  • Frangakis , C. E. , Rubin , D. B. ( 1999 ). Addressing complications of intention-to-treat analysis in the combined presence of all-or-none treatment-noncompliance and subsequent missing outcomes . Biometrika 86 : 365 – 379 .
  • Greenland , S. , Robins , J. M. ( 1985 ). Estimation of a common effect parameter from sparse follow-up data . Biometrics 41 : 55 – 68 .
  • Jo , B. ( 2002 ). Statistical power in randomized intervention studies with noncompliance . Psychological Methods 7 : 178 – 193 .
  • Little , R. J. A. , Rubin , D. B. ( 1987 ). Statistical Analysis with Missing Data . New York , NY : Wiley .
  • Lui , K.-J. ( 2002 ). Notes on estimation of the general odds ratio and the general risk difference for paired-sample data . Biometrical Journal 44 : 957 – 968 .
  • Lui , K.-J. ( 2004 ). Statistical Estimation of Epidemiological Risk . New York , NY : Wiley .
  • Lui , K.-J. ( 2005 ). Interval estimation of the difference in proportions under m-to-one matching . Statistics in Medicine 24 : 1765 – 1776 .
  • Lui , K.-J. ( 2007a ). Interval estimation of the risk difference in non-compliance randomized trials with repeated binary measurements . Statistics in Medicine 26 : 3140 – 3156 .
  • Lui , K.-J. ( 2007b ). Correcting for non-compliance of repeated binary outcomes in randomized clinical trials: randomized analysis approach. Statistics in Medicine (Letter to the Editor) 26:4679–4685 .
  • Lui , K.-J. ( 2008a ). Estimation of proportion ratio in non-compliance randomized trials with repeated measurements in binary data . Statistical Methodology 5 : 129 – 141 .
  • Lui , K.-J. ( 2008b ). Notes on interval estimation of risk difference in stratified noncompliance randomized trials: A Monte Carlo evaluation . Computational Statistics and Data Analysis 52 : 4091 – 4103 .
  • Lui , K.-J. ( 2011 ). Binary Data Analysis of Randomized Clinical Trials With Noncompliance . New York , NY : Wiley .
  • Lui , K.-J. , Chang , K.-C. ( 2008 ). Testing homogeneity of risk difference in stratified trials with noncompliance . Computational Statistics and Data Analysis 53 : 209 – 221 .
  • Matsui , S. (2005). Stratified analysis in randomized trials with noncompliance. Biometrics 61:816–823.
  • Matsuyama , Y. ( 2002 ). Correcting for non-compliance of repeated binary outcomes in randomized clinical trials: randomized analysis approach. Statistics in Medicine 21: 675–687 .
  • Multiple Risk factor Intervention Trial Research Group. ( 1982 ). Multiple risk factor intervention trial: risk factor changes and mortality results . Journal of the American Medical Association 248 : 1465 – 1477 .
  • Ohno , R. , Miyawaki , S. , Hatake , K. , Kuriyama , K. , Saito , K. , Kanamaru , A. , Kobayashi , T. , Kodera , Y. , Nishikawa , K. , Matsuda , S. , Yamada , O. , Omoto , E. , Takeyama , H. , Tsukuda , K. , Asou , N. , Tanimoto , M. , Shiozaki , H. , Tomonaga , M. , Masaoka , T. , Miura , Y. , Takaku , F. , Ohashi , Y. , Motoyoshi , K. ( 1997 ). Human urinary macrophage colony-stimulating factors reduces the incidence and duration of febrile neutropenia and shortens the period required to finish three courses of intensive consolidation therapy in acute myeloid leukemia: a double-blind controlled study . Journal of Clinical Oncology 15 : 2954 – 2965 .
  • Rubin , D. B. ( 1987 ). Multiple Imputation for Survey Nonresponse . New York , NY : Wiley .
  • SAS Institute , Inc. ( 1990 ). SAS Language Version . Cary , NC : SAS Institute, Inc .
  • Sato , T. ( 2000 ). Sample size calculations with compliance information . Statistics in Medicine 19 : 2689 – 2697 .
  • Sato , T. ( 2001 ). A method for the analysis of repeated binary outcomes in randomized Clinical trials with non-compliance . Statistics in Medicine 20 : 2761 – 2774 .
  • Schafer , J. L. ( 1997 ). Analysis of Incomplete Multivariate Data . London , UK : Chapman & Hall .
  • Sommer , A. , Zeger , S. L. ( 1991 ). On estimating efficacy from clinical trials . Statistics in Medicine 10 : 45 – 52 .
  • Walter , S. D. , Guyatt , G. , Montori , V. M. , Cook , R. , Prasad , K. ( 2006 ). A new preference-based analysis for randomized trials can estimate treatment acceptability and effect in compliant patients . Journal of Clinical Epidemiology 59 : 685 – 696 .
  • Zelen , M. ( 1979 ). A new design for randomized clinical trials . New England Journal of Medicine 300 : 1242 – 1245 .
  • Zelen , M. ( 1982 ). Strategy and alternate designs in cancer clinical trials . Cancer Treatment Reports 66 : 1095 – 1100 .
  • Zelen , M. ( 1990 ). Randomized consent designs for clinical trials: an update . Statistics in Medicine 9 : 645 – 656 .
  • Zhou , X. H. , Li , S. M. ( 2006 ). ITT analysis of randomized encouragement design studies with missing data . Statistics in Medicine 25 : 2737 – 2761 .

Reprints and Corporate Permissions

Please note: Selecting permissions does not provide access to the full text of the article, please see our help page How do I view content?

To request a reprint or corporate permissions for this article, please click on the relevant link below:

Academic Permissions

Please note: Selecting permissions does not provide access to the full text of the article, please see our help page How do I view content?

Obtain permissions instantly via Rightslink by clicking on the button below:

If you are unable to obtain permissions via Rightslink, please complete and submit this Permissions form. For more information, please visit our Permissions help page.