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Amyloid
The Journal of Protein Folding Disorders
Volume 12, 2005 - Issue 2
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Original Article

Multicentre versus single centre approach to rare diseases: The model of systemic light chain amyloidosis

Giovanni Palladini Amyloidosis Centre, IRCCS Policlinico San Matteo, University of Pavia, Pavia, Italy
,
Robert A Kyle Division of Hematology, Mayo Clinic, Rochester, Minnesota, USA
,
Dirk R Larson Division of Biostatistics, Mayo Clinic, Rochester, Minnesota, USA
,
Terry M Therneau Division of Biostatistics, Mayo Clinic, Rochester, Minnesota, USA
,
Giampaolo Merlini Amyloidosis Centre, IRCCS Policlinico San Matteo, University of Pavia, Pavia, Italy
&
Morie A Gertz Division of Hematology, Mayo Clinic, Rochester, Minnesota, USA
Pages 120-126 | Received 21 Jul 2003, Accepted 04 Nov 2004, Published online: 06 Jul 2009

References

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  • Comenzo RL, Vosburgh E, Falk RH, Sanchorawala V, Reisinger J, Dubrey S, et al. Dose-intensive melphalan with blood stem-cell support for the treatment of AL (amyloid light-chain) amyloidosis: Survival and responses in 25 patients. Blood 1998;91:3662–3670.
  • Moreau P, Leblond V, Bourquelot P, Facon T, Huynh A, Caillot D, et al. Prognostic factors for survival and response after high-dose therapy and autologous stem cell transplantation in systemic AL amyloidosis: A report on 21 patients. Br J Haematol 1998;101:766–769.
  • Merlini G. Symposium on amyloid cardiomyopathy: Diagnosis and treatment, Pavia, September 21, 1996. Amyloid 1997;4:296–299.

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