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Expert Opinion on Orphan Drugs Volume 5, 2017 - Issue 1
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Editorial

Therapeutic targets in homocystinuria due to cystathionine β-synthase deficiency: new European guidelines

Bridget WilckenPhysician, Genetic Metabolic Service, Sydney Children’s Hospital, Randwick, Australia;Honorary Consultant, NSW Biochemical Genetics and Newborn Screening Services, The Children’s Hospital at Westmead; and University of Sydney, Sydney, AustraliaCorrespondence[email protected]; [email protected]
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Pages 1-3 | Received 25 Oct 2016, Accepted 08 Nov 2016, Published online: 21 Nov 2016

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