Estimating and Testing Treatment Effects on Two Binary Endpoints and Association Between Endpoints in Clinical Trials

References

• Adams , H. P. , Woolson , R. F. , Clarke , W. R. , Davis , P. H. , Bendixen , B. H. , Love , B. B. , Wasek , P. A. , Grimsman , K. J. ( 1997 ). Design of the trial of Org 10172 in acute stroke treatment . Controlled Clin. Trials 18 : 358 – 377 . [PUBMED] [INFOTRIEVE] [CSA]
   PubMedGoogle Scholar
• Agresti , A. , Lipsitz , S. R. , Lang , J. B. ( 1991 ). Analysis of sparse repeated categorical measurement data . Proc. 16th Ann. SAS User's Group Int. Conf. Cary , North Carolina , SAS Institute Inc. , pp. 1452 – 1460 .
   Google Scholar
• Birnbaum , A. ( 1954 ). Combining independent tests of significance . JASA 49 : 559 – 574 .
   Web of Science ®Google Scholar
• Brott , T. , Adams , H. P. , Jr. , Olinger , C. P. , Marler , J. R. , Barsan , W. G. , Biller , J. , Spilker , J. , Holleran , R. , Eberle , R. , Hertzberg , V. ( 1989 ). Measurements of acute cerebral infarction. A clinical examination scale . Stroke 20 : 864 – 870 . [PUBMED] [INFOTRIEVE]
   PubMed Web of Science ®Google Scholar
• Carey , V. , Zeger , S. L. , Diggle , P. ( 1993 ). Modeling multivariate binary data with alternating logistic regressions . Biometrika 80 : 517 – 526 .
   Web of Science ®Google Scholar
• Fisher , R. A. ( 1958 ). Statistical Methods for Research Workers. , 13th ed. Section 21.1 , pp. 99 – 101 .
   Google Scholar
• Fitzmaurice , G. M. , Laird , N. M. ( 1993 ). A likelihood-based method for analyzing longitudinal binary responses . Biometrika 80 : 141 – 151 .
   Web of Science ®Google Scholar
• Grizzle , J. E. ( 1971 ). Multivariate logit analysis . Biometrics 27 : 1057 – 1062 . [PUBMED] [INFOTRIEVE]
   PubMed Web of Science ®Google Scholar
• Grizzle , J. E. , Starmer , F. , Koch , G. G. ( 1969 ). Analysis of categorical data by linear models . Biometrics 25 : 489 – 504 . [PUBMED] [INFOTRIEVE]
   PubMed Web of Science ®Google Scholar
• Hartung , J. ( 1999 ). A note on combining dependent tests of significance . Biometrical J. 41 : 849 – 855 . [CROSSREF]
   Web of Science ®Google Scholar
• Jennet , B. , Bond , M. ( 1975 ). Assessment of outcome after severe brain damage. A practical scale . Lancet 1 : 480 – 484 . [CROSSREF]
   PubMed Web of Science ®Google Scholar
• Koch , G. G. , Landis , J. R. , Freeman , J. L. , Freeman , D. H. , Jr. , Lehnen , R. G. ( 1977 ). A general methodology for the analysis of experiments with repeated measurement of categorical data . Biometrics 33 : 133 – 158 . [PUBMED] [INFOTRIEVE]
   PubMed Web of Science ®Google Scholar
• Koch , G. G. , Amara , I. A. , Davis , G. W. , Gillings , D. B. ( 1982 ). A review of some statistical methods for covariance analysis of categorical data . Biometrics 38 : 563 – 595 . [PUBMED] [INFOTRIEVE]
   PubMed Web of Science ®Google Scholar
• Liang , K. Y. , Zeger , S. L. ( 1986 ). Longitudinal data analysis using generalized linear models . Biometrika 73 : 13 – 22 .
   Web of Science ®Google Scholar
• Lipsitz , S. R. , Laird , N. M. , Harrington , D. P. ( 1990 ). Maximum likelihood regression methods for paired binary data . Statist. Med. 9 : 1517 – 1525 .
   PubMed Web of Science ®Google Scholar
• Lipsitz , S. R. , Laird , N. M. , Harrington , D. P. ( 1991 ). Generalized estimating equations for correlated binary data: using the odds ratio as a measure of association . Biometrika 78 : 153 – 160 .
   Web of Science ®Google Scholar
• Mahoney , F. I. , Barthel , D. W. ( 1965 ). Function evaluation. The Barthel index . Maryland State Medical J. 14 : 61 – 65 .
   PubMedGoogle Scholar
• Miller , M. E. , Davis , C. S. , Landis , J. R. ( 1993 ). The analysis of longitudinal polytomous data: generalized estimating equations and connections with weighted least squares . Biometrics 49 : 1033 – 1044 . [PUBMED] [INFOTRIEVE]
   PubMed Web of Science ®Google Scholar
• Molenberghs , G. , Ritter , L. L. ( 1996 ). Methods for analyzing multivariate binary data, with association between outcomes of interest . Biometrics 52 : 1121 – 1133 . [PUBMED] [INFOTRIEVE] [CSA]
   PubMed Web of Science ®Google Scholar
• Pagano , M. , Gauvreau , K. ( 2000 ). Principles of Biostatistics. , 2nd ed. Pacific Grove , California : Duxbury Press , pp. 381 – 386 .
   Google Scholar
• Park , T. (1993). A comparison of the generalized estimating equation approach with the maximum likelihood approach for repeated measurements. Statist. Med. 12:1723–32.
   PubMed Web of Science ®Google Scholar
• Prentice , R. L. , Zhao , L. P. ( 1991 ). Estimating equations for parameters in means and covariances of multivariate discrete and continuous responses . Biometrics 47 : 825 – 839 . [PUBMED] [INFOTRIEVE]
   PubMed Web of Science ®Google Scholar
• Rosner , B. ( 1995a ). Fundamentals of Biostatics. , 4th ed. Belmont , California : Duxbury Press , pp. 346 – 348 .
   Google Scholar
• Rosner , B. ( 1995b ). Fundamentals of Biostatics. , 4th ed. Belmont , California : Duxbury Press , pp. 314 – 317 .
   Google Scholar
• Ten Have , T. R. , Morabia , A. ( 1999 ). Mixed effects models with bivariate and univariate association parameters for longitudinal bivariate binary response data . Biometrics 55 ( 1 ): 85 – 93 . [PUBMED] [INFOTRIEVE] [CSA] [CROSSREF]
   PubMed Web of Science ®Google Scholar
• van Zwet , W. R. , Oosterhoff , J. ( 1967 ). On the combination of independent test statistics . Ann. Mathemat. Statist. 38 : 659 – 680 .
   Google Scholar
• Wade , D. T. ( 1992 ). Measurement in Neurological Rehabilitation . Oxford : Oxford University Press , pp. 177 – 178 , 237 – 238 .
   Google Scholar
• Wallis , W. A. ( 1942 ). Compounding probabilities from independent significance tests . Econometrica 10 : 229 – 248 .
   Google Scholar
• Zeger , S. L. , Liang , K. Y. ( 1986 ). Longitudinal data analysis for discrete and continuous outcomes . Biometrics 42 : 121 – 130 . [PUBMED] [INFOTRIEVE]
   PubMed Web of Science ®Google Scholar
• Zhao , L. P. , Prentice , R. L. ( 1990 ). Correlated binary regression using a quadratic exponential model . Biometrika 77 : 642 – 648 .
   Web of Science ®Google Scholar
• Zhao , L. P. , Prentice , R. L. , Self , S. G. ( 1992 ). Multivariate mean parameter estimation by using a partly exponential model . J. Roy. Statist. Soc. Ser. B ( Methodological ) 54 : 805 – 811 .
   Google Scholar