Bibliography
- European Organisation for Rare Diseases (EURORDIS). Available from: www.eurordis.org [Last accessed 24 September 2014]
- European Medicines Agency (EMA). orphan Designation section. Available from: www.ema.europa.eu/ema/index.jsp?curl=pages/regulation/general/general_content_000029.jsp&mid=WC0b01ac05800240ce [Last accessed 24 September 2014]
- EMA. Pharmacovigilance section. Available from: www.ema.europa.eu/ema/index.jsp?curl=pages/regulation/general/general_content_000145.jsp&mid=WC0b01ac058002708a [Last accessed 24 September 2014]
- EMA. Scientific Advice and Protocol Assistance section. Available from: www.ema.europa.eu/ema/index.jsp?curl=pages/regulation/general/general_content_ 000049.jsp&mid=WC0b01ac05800 229b9 [Last accessed 24 September 2014]
- EMA. Biomarkers section. Available from: www.ema.europa.eu/ema/index.jsp?curl=pages/special_topics/general/general_content_000349.jsp&mid=WC0b01ac05800baedb [Last accessed 24 September 2014]
- International Rare Disease Research Consortium (IRDiRC). Available from: www.irdirc.org [Last accessed 24 September 2014]
- Rare Disease Day 2014. Available from: www.rarediseaseday.org [Last accessed 24 September 2014]