1,221
Views
10
CrossRef citations to date
0
Altmetric
ORIGINAL ARTICLE

The cost-effectiveness of somatropin treatment for short children born small for gestational age (SGA) and children with growth hormone deficiency (GHD) in Sweden

, , &
Pages 168-178 | Published online: 08 Feb 2010

References

  • Clayton PE, Cianfarani S, Czernichow P, Management of the child born small for gestational age through to adulthood: a consensus statement of the International Societies of Pediatric Endocrinology and the Growth Hormone Research Society. J Clin Endocrinol Metab 2007;92:804-10.
  • Barker DJ, Hales CN, Fall CH, Type 2 (non-insulin- dependent) diabetes mellitus, hypertension and hyperlipidaemia (syndrome X): relation to reduced fetal growth. Diabetologia 1993;36:62-7.
  • Karlberg J, Albertsson-Wikland K. Growth in full-term small-for-gestational-age infants: from birth to final height. Pediatr Res 1995;38:733-9.
  • Hinchliffe SA, Lynch MR, Sargent PH, The effect of intrauterine growth retardation on the development of renal nephrons. Br J Obstet Gynaecol 1992;99:296-301.
  • Hales CN, Barker DJ, Clark PM, Fetal and infant growth and impaired glucose tolerance at age 64. BMJ 1991;303:1019-22
  • Osmond C, Barker DJ, Winter PD, Early growth and death from cardiovascular disease in women. BMJ 1993;307:1519-24
  • Ibanez L, Potau N, Ferrer A, Reduced ovulation rate in adolescent girls born small for gestational age. J Clin Endocrinol Metab 2002;87:3391-3.
  • Barker DJ, Godfrey KM, Fall C, Relation of birth weight and childhood respiratory infection to adult lung function and death from chronic obstructive airways disease. BMJ 1991;303:671-5
  • Novo Nordisk Limited. Available at: http://www.novonordisk.co.uk/documents/article_page/document/ght_facts_children_sga.asps. s(Last accessed June 2007)
  • Hokken-Koelega AC, De ridder MA, Lemmen RJ, Children born small for gestational age: do they catch up? Pediatr Res 1995;38:267-71.
  • Growth Hormone Research Society. Consensus guidelines for the diagnosis and treatment of growth hormone (GH) deficiency in childhood and adolescence: summary statement of the GH Research Society. J Clin Endocrinol Metab 2000;85:3990-3.
  • Christensen TL, Djurhuus CB, Clayton P, An evaluation of the relationship between adult height and health-related quality of life in the general UK population. Clin Endocrinol 2007;67:407-12.
  • Verrips G, Vogels A, Koopman H, Measuring health related quality of life in a child population. Eur J Publ 1999;9:188-93.
  • Phillips C, Thompson G. What is a QALY? Available at http://www.medicine.ox.ac.uk/bandolier/painres/download/whatis/QALY.pdf. (Last accessed November 2009)
  • Persson U, Hjelmgren J. Health services need knowledge of how the public values health. Lakartidningen 2003;100:3436-7.
  • Bannink EM, van Doorn J, Mulder PG, Free/dissociable insulin-like growth factor (IGF)-I, not total IGF-I, correlates with growth response during growth hormone treatment in children born small for gestational age. J Clin Endocrinol Metab 2007;92:2992-3000.
  • Novo Nordisk Limited. GHRETARD/BPD/14-20-21/NL clinical trial. Unpublished data 2007
  • Statistics Sweden (Statistiska centralbyran). Available at: http://www.scb.se/. (Last accessed January 2010).
  • van Pareren Y, Mulder P, Houdijk M, Adult height after long-term, continuous growth hormone (GH) treatment in short children born small for gestational age: results of a randomized, double-blind, dose-response GH trial. J Clin Endocrinol Metab 2003;88:3584-90.
  • The Pharmaceutical Benefits Board. General guidelines for economic evaluations from the Pharmaceutical Benefits Board (LFNAR 2003:2). Available at: http://www.ispor.org/peguidelines/source/Guidelines_in_Sweden.pdf. (Last accessed November 2009)
  • Novo Nordisk Limited. Norditropin summary of product characteristics. Available at: http://emc.medicines.org.uk/medicine/2760/SPC/Norditropin SimpleXx 5 mg/1.5 ml, Norditropin SimpleXx 10 mg/1.5 ml, Norditropin SimpleXx 15 mg/1.5 ml. (Last accessed January 2010)
  • Bryant J, Cave C, Mihaylova B, Clinical effectiveness and cost-effectiveness of growth hormone in children: a systematic review and economic evaluation. Health Technol Assess 2002;6:1-168.
  • Cutfield WS, Karagiannis G, Reiter EO. GH treatment to final height in idiopathic GH deficiency: The KIGS experience. In: Ranke MB, Price DA, Reiter EO, eds. Growth Hormone Therapy in Pediatrics – 20 years of KIGS. Basel: Karger 2007;145-62.
  • August GP, Julius JR, Blethen SL. Adult height in children with growth hormone deficiency who are treated with biosynthetic growth hormone: the National Cooperative Growth Study experience. Pediatrics 1998;102:512-16.
  • Carel JC, Ecosse E, Nicolino M, Adult height after long term treatment with recombinant growth hormone for idiopathic isolated growth hormone deficiency: observational follow up study of the French population based registry. BMJ 2002;325:70
  • de Ridder MA, Stijnen T, Hokken-Koelega AC. Prediction of adult height in growth-hormone-treated children with growth hormone deficiency. J Clin Endocrinol Metab 2007;92:925-31.
  • Harris M, Hofman PL, Cutfield WS. Growth hormone treatment in children: review of safety and efficacy. Paediatr Drugs 2004:6:93-106
  • The European Agency for the Evaluation of Medicinal Products. Committee for Proprietary Medicinal Products (CPMP) opinion following an article (75) referal - Norditropin. Available at: http://www.ema.europa.eu/pdfs/human/referral/norditropin/347803en.pdf. (Last accessed January 2010)
  • Endocrinology list prices in Sweden. Available at: http://www.externt9.lul.se/svn/akademiska09.xls. (Last accessed November 2009)
  • FASS. Available at: http://www.fass.se/LIF/home/soktraffar_all.jsp?searchtext1=norditropin&searchtext2=&allCategories=false&searchtype=. (Last accessed November 2009)
  • Lustig RH. Optimizing growth hormone efficacy: an evidence-based analysis. Horm Res 2004;62(Suppl 3):93-7.
  • The EuroQol Group. EuroQol – a new facility for the measurement of health-related quality of life. Health Policy 1990;16: 199-208.
  • Dolan P, Gudex C, Kind P, A social tariff for EuroQol: results from a UK general population survey. Working Papers 138, September 1995. Centre for Health Economics, University of York. Available at: http://www.york.ac.uk/inst/che/pdf/DP138.pdf. (Last accessed November 2009)
  • Pal DK. Quality of life assessment in children: a review of conceptual and methodological issues in multidimensional health status measures. J Epidemiol Community Health 1996;50:391-6.
  • The National Institute for Health and Clinical Excellence (NICE). Guidance on the use of human growth hormone (somatropin) in children with growth failure. Technology Appraisal No. 42, May 2002. Available at: http://www.nice.org.uk/nicemedia/pdf/HGHinChild-42-ALS.pdf. (Last accessed November 2009).
  • Bannink EM, van Pareren YK, Theunissen NC, Quality of life in adolescents born small for gestational age: does growth hormone make a difference? Horm Res 2005;64:166-74.
  • Fayter DA, Nixon J, Hartley S, Effectiveness and cost-effectiveness of height screening programmes during the primary school years: a systematic review. Arch Dis Child 2007;93:278-84.
  • Sandberg D, Colsman, M. Assessment of psychosocial aspects of short stature. Growth Genet Horm 2005;21:17-25.
  • Schwarzinger M, Stouthard ME, Burstrom K, Cross-national agreement on disability weights: the European Disability Weights Project. Popul Health Metr 2003;1:9
  • Kirk J, Butler G, (BSPED). Treatment of Children with Recombinant Human Growth Hormone (r-hGH). Shared Care Guidelines April 2006. Available at: http://www.bsped.org.uk/professional/guidelines/docs/SharedcareGH-BSPED.pdf. (Last accessed November 2009).
  • Sheiner E, Levy A, Katz M, Short stature – an independent risk factor for Cesarean delivery. Eur J Obstet Gynecol Reprod Biol 2005;120:175-8.
  • Wheeler PG, Bresnahan K, Shephard BA, Short stature and functional impairment: a systematic review. Arch Pediatr Adolesc Med 2004;158:236-43.
  • Wake M, Coghlan D, Hesketh K. Does height influence progression through primary school grades? Arch Dis Child 2000;82: 297-301.
  • Lundgren EM, Cnattingius S, Jonsson B, Birth characteristics and different dimensions of intellectual performance in young males: a nationwide population-based study. Acta Paediatr 2003;92:1138-43.
  • Barker DJ, Eriksson JG, Forsen T, Infant growth and income 50 years later. Arch Dis Child 2005;90:272-3.
  • Magnusson PK, Gunnell D, Tynelius P, Strong inverse association between height and suicide in a large cohort of Swedish men: evidence of early life origins of suicidal behavior? Am J Psychiatry 2005;162:1373-5.
  • Mittendorfer-Rutz E, Wasserman D, Rasmussen FF. Fetal and childhood growth and the risk of violent and non-violent suicide attempts: a cohort study of 318,953 men. J Epidemiol Commun Health 2008;62:168-73.

Reprints and Corporate Permissions

Please note: Selecting permissions does not provide access to the full text of the article, please see our help page How do I view content?

To request a reprint or corporate permissions for this article, please click on the relevant link below:

Academic Permissions

Please note: Selecting permissions does not provide access to the full text of the article, please see our help page How do I view content?

Obtain permissions instantly via Rightslink by clicking on the button below:

If you are unable to obtain permissions via Rightslink, please complete and submit this Permissions form. For more information, please visit our Permissions help page.