Statistics in Biopharmaceutical Research, Volume 16, Issue 1 (2024)

Browse this journal
Sample our Mathematics & Statistics journals, sign in here to start your FREE access for 14 days

Statistics in Biopharmaceutical Research, Volume 16, Issue 1 (2024)

See all volumes and issues
Volume 16, 2024 Vol 15, 2023 Vol 14, 2022 Vol 13, 2021 Vol 12, 2020 Vol 11, 2019 Vol 10, 2018 Vol 9, 2017 Vol 8, 2016 Vol 7, 2015 Vol 6, 2014 Vol 5, 2013 Vol 4, 2012 Vol 3, 2011 Vol 2, 2010 Vol 1, 2009
Download citations Download PDFs Download issue

Research Articles

Article
Combining the Target Trial and Estimand Frameworks to Define the Causal Estimand: An Application Using Real-World Data to Contextualize a Single-Arm Trial
Lisa V. Hampson, Jufen Chu, Aiesha Zia, Jie Zhang, Wei-Chun Hsu, Craig S. Parzynski, Yanni Hao & Evgeny Degtyarev
Pages: 1-10
Published online: 13 Apr 2023
AbstractforCombining the Target Trial and Estimand Frameworks to Define the Causal Estimand: An Application Using Real-World Data to Contextualize a Single-Arm Trial | Full Text | References | PDF (1.2 MB) | EPUB
  • 618 Views
  • 2 CrossRef citations
  • 0Altmetric
Article
Targeted Learning: Toward a Future Informed by Real-World Evidence
Susan Gruber, Rachael V. Phillips, Hana Lee, Martin Ho, John Concato & Mark J. van der Laan
Pages: 11-25
Published online: 15 Mar 2023
AbstractforTargeted Learning: Toward a Future Informed by Real-World Evidence | Full Text | References | PDF (1.6 MB) | EPUB | Supplemental
  • 636 Views
  • 8 CrossRef citations
  • 0Altmetric
Article
Examples of Applying RWE Causal-Inference Roadmap to Clinical Studies
Martin Ho, Susan Gruber, Yixin Fang, Douglas E. Faris, Pallavi Mishra-Kalyani, David Benkeser & Mark van der Laan
Pages: 26-39
Published online: 21 Mar 2023
AbstractforExamples of Applying RWE Causal-Inference Roadmap to Clinical Studies | Full Text | References | PDF (1.6 MB) | EPUB
  • 588 Views
  • 0 CrossRef citations
  • 0Altmetric
Article
Joint Analysis of Longitudinal Data and Zero-Inflated Recurrent Events
Chenchen Ma & Kimberly Crimin
Pages: 40-46
Published online: 10 Mar 2023
AbstractforJoint Analysis of Longitudinal Data and Zero-Inflated Recurrent Events | Full Text | References | PDF (747.5 KB) | EPUB | Supplemental
  • 175 Views
  • 0 CrossRef citations
  • 0Altmetric
Article
Methods for Informative Censoring in Time-to-Event Data Analysis
Man Jin & Yixin Fang
Pages: 47-54
Published online: 15 Mar 2023
AbstractforMethods for Informative Censoring in Time-to-Event Data Analysis | Full Text | References | PDF (750 KB) | EPUB
  • 503 Views
  • 2 CrossRef citations
  • 0Altmetric
Article
Adaptive Endpoints Selection with Application in Rare Disease
Heng Xu, Yi Liu & Robert A. Beckman
Pages: 55-63
Published online: 07 Apr 2023
AbstractforAdaptive Endpoints Selection with Application in Rare Disease | Full Text | References | PDF (975.4 KB) | EPUB | Supplemental
  • 252 Views
  • 1 CrossRef citations
  • 0Altmetric
Article
A Test of the Dependence Assumptions for the Simes-Test-based Multiple Test Procedures
Jiangtao Gou
Pages: 64-70
Published online: 13 Apr 2023
AbstractforA Test of the Dependence Assumptions for the Simes-Test-based Multiple Test Procedures | Full Text | References | PDF (1,019.2 KB) | EPUB
  • 149 Views
  • 1 CrossRef citations
  • 0Altmetric
Article
Copula-Based Model for Incorporating Single-Agent Historical Data into Dual-Agent Phase I Cancer Trials
Koichi Hashizume, Jun Tsuchida & Takashi Sozu
Pages: 71-88
Published online: 14 Apr 2023
AbstractforCopula-Based Model for Incorporating Single-Agent Historical Data into Dual-Agent Phase I Cancer Trials | Full Text | References | PDF (3.5 MB) | EPUB
  • 198 Views
  • 1 CrossRef citations
  • 0Altmetric
Article
Bayesian Borrowing Methods for Count Data: Analysis of Incontinence Episodes in Patients with Overactive Bladder
Akalu Banbeta, Emmanuel Lesaffre, Reynaldo Martina & Joost van Rosmalen
Pages: 89-103
Published online: 13 Apr 2023
AbstractforBayesian Borrowing Methods for Count Data: Analysis of Incontinence Episodes in Patients with Overactive Bladder | Full Text | References | PDF (1.8 MB) | EPUB
  • 213 Views
  • 0 CrossRef citations
  • 0Altmetric
Article
Some Multiplicity Adjustment Procedures for Clinical Trials with Sequential Design and Multiple Endpoints
Xiaodong Luo & Hui Quan
Pages: 104-115
Published online: 14 Apr 2023
AbstractforSome Multiplicity Adjustment Procedures for Clinical Trials with Sequential Design and Multiple Endpoints | Full Text | References | PDF (1.1 MB) | EPUB | Supplemental
  • 244 Views
  • 1 CrossRef citations
  • 0Altmetric
Article
Multiply Robust Weighted Generalized Estimating Equations for Incomplete Longitudinal Binary Data Using Empirical Likelihood
Hiroshi Komazaki, Masaaki Doi, Naohiro Yonemoto & Tosiya Sato
Pages: 116-129
Published online: 18 Apr 2023
AbstractforMultiply Robust Weighted Generalized Estimating Equations for Incomplete Longitudinal Binary Data Using Empirical Likelihood | Full Text | References | PDF (2.1 MB) | EPUB | Supplemental
  • 117 Views
  • 0 CrossRef citations
  • 0Altmetric
Article
Application of Group Sequential Methods to the 2-in-1 Design and Its Extensions for Interim Monitoring
Xuekui Zhang, Haijun Jia, Li Xing & Cong Chen
Pages: 130-139
Published online: 18 Apr 2023
AbstractforApplication of Group Sequential Methods to the 2-in-1 Design and Its Extensions for Interim Monitoring | Full Text | References | PDF (1.3 MB) | EPUB
  • 234 Views
  • 4 CrossRef citations
  • 0Altmetric
Correction
Correction
Page: 140
Published online: 01 Feb 2024
CitationforCorrection | Full Text | PDF (142 KB) | EPUB
  • 140 Views
  • 0 CrossRef citations
  • 0Altmetric
Free Access

Back Matter

Statistics in Biopharmaceutical Research 2023 Associate Editors
Page: i
Published online: 01 Feb 2024
CitationforStatistics in Biopharmaceutical Research 2023 Associate Editors | Full Text | PDF (131.3 KB) | EPUB
  • 117 Views
  • 0 CrossRef citations
  • 0Altmetric
Free Access

Explore articles

Explore the most recently published articles

Trial Design with Win Statistics for Multiple Time-to-Event Endpoints with Hierarchy
Huiman X. Barnhart et al.
Article | Published online: 15 Jul 2024
Unsupervised Imputation of Non-Ignorably Missing Data Using Importance-Weighted Autoencoders
David K. Lim et al.
Article | Published online: 15 Jul 2024
MT-Keyboard: A Bayesian Model-assisted Interval Design to Account for Toxicity Grades and Types for Phase I Trials
Kai Chen et al.
Article | Published online: 26 Jun 2024
Possible data-generating models of longitudinal continuous outcomes and intercurrent events to investigate estimands
Marian Mitroiu et al.
Article | Published online: 26 Jun 2024
Open Access
View all latest articles