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Editorial

Big Pharma's new model in orphan drugs and rare diseases

, PhD, DSc, FAHA (Norris Professor of Life Sciences, Director)
Pages 1-3 | Published online: 17 Dec 2012

Bibliography

  • Cote T, Kelkar A, Xu K, Orphan products: an emerging trend in drug approvals. Nat Rev Drug Discov 2010;9(1):84
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  • Thorat C, Xu K, Freeman SN, What the orphan drug act has done lately for children with rare diseases: a 10-year analysis. Pediatrics 2012;129(3):516-21
  • Herper M. How a $440,000 drug is turning Alexion into a biotech's new innovation powerhouse. Forbes; 2012

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