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Original Research

An indirect treatment comparison of the efficacy of patisiran and tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathy

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Pages 473-481 | Received 23 Oct 2018, Accepted 28 Nov 2018, Published online: 12 Dec 2018

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Read on this site (6)

Madeline Merkel, David Danese, Chongshu Chen, Jessie Wang, Aozhou Wu, Hongbo Yang & Hollis Lin. (2023) Indirect treatment comparison (ITC) of the efficacy of vutrisiran and tafamidis for hereditary transthyretin-mediated amyloidosis with polyneuropathy. Expert Opinion on Pharmacotherapy 24:10, pages 1205-1214.
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Ana Peláez Bejarano, Maria de las Aguas Robustillo Cortés & Maria Isabel Guzman Ramos. (2021) Patient experience in a rare disease: application of the IEXPAC questionnaire in hereditary transthyretin-mediated amyloidosis. Expert Opinion on Orphan Drugs 9:6, pages 175-180.
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Peter Gorevic, Jaclyn Franklin, Jihong Chen, Gautam Sajeev, Jessie C. H. Wang & Hollis Lin. (2021) Indirect treatment comparison of the efficacy of patisiran and inotersen for hereditary transthyretin-mediated amyloidosis with polyneuropathy. Expert Opinion on Pharmacotherapy 22:1, pages 121-129.
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Imtiaz A. Samjoo, Elizabeth M. Salvo, Diana Tran, Leslie Amass, Michelle Stewart & Chris Cameron. (2020) The impact of clinical heterogeneity on conducting network meta-analyses in transthyretin amyloidosis with polyneuropathy. Current Medical Research and Opinion 36:5, pages 799-808.
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Hollis Lin, Sonalee Agarwal, Marissa Betts, Kyle Fahrbach, Madhura Chitnis & Michael Polydefkis. (2019) Response to the letter to the editor on “an indirect treatment comparison of the efficacy of patisiran and tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathy”. Expert Opinion on Pharmacotherapy 20:12, pages 1529-1530.
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Articles from other publishers (15)

Osnat Itzhaki Ben Zadok & Rodney H. Falk. (2023) Variant and wild type transthyretin amyloidosis: two sides of the same coin or different currencies in different pockets?. European Journal of Heart Failure 25:4, pages 525-527.
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Efthimios Dardiotis & Theodoros Kyriakides. (2023) Drug and Gene Therapy for Treating Variant Transthyretin Amyloidosis (ATTRv) Neuropathy. Current Neuropharmacology 21:3, pages 471-481.
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Intissar Anan, Ole B. Suhr, Katarzyna Liszewska, Jorge Mejia Baranda, Björn Pilebro, Jonas Wixner & Elisabet Ihse. (2022) Amyloid fibril composition type is consistent over time in patients with Val30Met (p.Val50Met) transthyretin amyloidosis. PLOS ONE 17:3, pages e0266092.
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Can Ebru Bekircan-Kurt, Ezgi Yilmaz, Doruk Arslan, Fatma Gokcem Yildiz, Özlem Dikmetas, Zeynep Ergul-Ulger, Sibel Kocabeyoglu, Murat Irkec, Vedat Hekimsoy, Lale Tokgozoglu, Ersin Tan & Sevim Erdem-Ozdamar. (2022) The functional and structural evaluation of small fibers in asymptomatic carriers of TTR p.Val50Met (Val30Met) mutation. Neuromuscular Disorders 32:1, pages 50-56.
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Bin Zhong, Xianhua Huang, Yizhou Zheng, Xiaohua Guo & Longhuo Wu. (2021) The discovery and development of transthyretin amyloidogenesis inhibitors: what are the lessons?. Future Medicinal Chemistry 13:23, pages 2083-2105.
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Massimo Russo, Luca Gentile, Vincenzo Di Stefano, Gianluca Di Bella, Fabio Minutoli, Antonio Toscano, Filippo Brighina, Giuseppe Vita & Anna Mazzeo. (2021) Use of Drugs for ATTRv Amyloidosis in the Real World: How Therapy Is Changing Survival in a Non-Endemic Area. Brain Sciences 11:5, pages 545.
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Luca Gentile, Massimo Russo, Marco Luigetti, Giulia Bisogni, Andrea Di Paolantonio, Angela Romano, Valeria Guglielmino, Ilenia Arimatea, Mario Sabatelli, Antonio Toscano, Giuseppe Vita & Anna Mazzeo. (2021) Patisiran in hATTR Amyloidosis: Six-Month Latency Period before Efficacy. Brain Sciences 11:4, pages 515.
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Meissane Benbrahim, Kelsey Norman, Vaishali Sanchorawala, Omar K Siddiqi & David Hughes. (2021) A review of novel agents and clinical considerations in patients with ATTR cardiac amyloidosis. Journal of Cardiovascular Pharmacology Publish Ahead of Print.
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Ivan Urits, Daniel Swanson, Michael C. Swett, Anjana Patel, Kevin Berardino, Ariunzaya Amgalan, Amnon A. Berger, Hisham Kassem, Alan D. Kaye & Omar Viswanath. (2020) A Review of Patisiran (ONPATTRO®) for the Treatment of Polyneuropathy in People with Hereditary Transthyretin Amyloidosis. Neurology and Therapy 9:2, pages 301-315.
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Hollis Lin, Madeline Merkel, Cecilia Hale & Jing L Marantz. (2020) Experience of patisiran with transthyretin stabilizers in patients with hereditary transthyretin-mediated amyloidosis. Neurodegenerative Disease Management 10:5, pages 289-300.
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Simoneide S. Titze-de-Almeida, Pedro Renato de Paula Brandão, Ingrid Faber & Ricardo Titze-de-Almeida. (2019) Leading RNA Interference Therapeutics Part 1: Silencing Hereditary Transthyretin Amyloidosis, with a Focus on Patisiran. Molecular Diagnosis & Therapy 24:1, pages 49-59.
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Saša A Živković. (2020) Neuropathy Associated with Hereditary Transthyretin Amyloidosis—Diagnosis and Management. US Neurology 16:2, pages 103.
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Yuhua Weng, Haihua Xiao, Jinchao Zhang, Xing-Jie Liang & Yuanyu Huang. (2019) RNAi therapeutic and its innovative biotechnological evolution. Biotechnology Advances 37:5, pages 801-825.
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Yvette N. Lamb & Emma D. Deeks. (2019) Tafamidis: A Review in Transthyretin Amyloidosis with Polyneuropathy. Drugs 79:8, pages 863-874.
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Giuseppe Vita, Gian Luca Vita, Claudia Stancanelli, Luca Gentile, Massimo Russo & Anna Mazzeo. (2019) Genetic neuromuscular disorders: living the era of a therapeutic revolution. Part 1: peripheral neuropathies. Neurological Sciences 40:4, pages 661-669.
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