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Degenerative Neurological and Neuromuscular Disease Volume 9, 2019 - Issue
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Review

Orphan Drugs In Development For The Treatment Of Friedreich’s Ataxia: Focus On Omaveloxolone

Shaila D Ghanekar1 University of South Florida (USF), Department of Neurology, Tampa, FL, USA;2 USF Ataxia Research Center, Department of Neurology, Tampa, FL, USA
,
Wai Wai Miller1 University of South Florida (USF), Department of Neurology, Tampa, FL, USA;2 USF Ataxia Research Center, Department of Neurology, Tampa, FL, USA;3 USF Movement Disorders Neuromodulation Center, Department of Neurology, Tampa, FL, USAORCID Iconhttps://orcid.org/0000-0003-2913-6676
ORCID Icon,
Colin J Meyer4 Reata Pharmaceuticals, Inc., Department of Product Development, Irving, TX, USA
,
Kevin J Fenelon1 University of South Florida (USF), Department of Neurology, Tampa, FL, USA;2 USF Ataxia Research Center, Department of Neurology, Tampa, FL, USA
,
Alvin Lacdao1 University of South Florida (USF), Department of Neurology, Tampa, FL, USA;2 USF Ataxia Research Center, Department of Neurology, Tampa, FL, USA
&
Theresa A Zesiewicz1 University of South Florida (USF), Department of Neurology, Tampa, FL, USA;2 USF Ataxia Research Center, Department of Neurology, Tampa, FL, USA;3 USF Movement Disorders Neuromodulation Center, Department of Neurology, Tampa, FL, USA;5 James A. Haley Veterans’ Hospital, Department of Neurology, Tampa, FL, USACorrespondence[email protected]
Pages 103-107 | Published online: 15 Oct 2019

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