Identifying a subpopulation with higher likelihoods of early response to treatment in a heterogeneous rare disease: a post hoc study of response to teduglutide for short bowel syndrome

Kristina S Chen1 Outcomes Research and Epidemiology, Shire Human Genetic Therapies, Inc., Cambridge, MA, USA, [email protected]Correspondence[email protected]

Jipan Xie2 Analysis Group, Inc., Los Angeles, CA, USA

Wenxi Tang3 Analysis Group, Inc., New York, NY, USA

Jing Zhao4 Analysis Group, Inc., Boston, MA, USA

Palle B Jeppesen5 Department of Medical Gastroenterology, Rigshospitalet, Copenhagen, Denmark

James E Signorovitch4 Analysis Group, Inc., Boston, MA, USA

Pages 1267-1277 | Published online: 25 Jul 2018

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Identifying a subpopulation with higher likelihoods of early response to treatment in a heterogeneous rare disease: a post hoc study of response to teduglutide for short bowel syndrome

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