Browse
We’re here to help

Find guidance on Author Services

Cart Add to Cart

Search
Browse
We’re here to help

Find guidance on Author Services

Home
All Journals
Expert Opinion on Orphan Drugs
List of Issues
Volume 9, Issue 7-10

Expert Opinion on Orphan Drugs

Search in:

Advanced search Citation search

Citation search

Ready to submit?
Start a new submission or continue a submission in progress
Go to submission site
Instructions for authors
Editorial policies
Editing services site

Journal metrics
Aims & scope
Journal information
Editorial board
News & calls for papers
Advertising information

Current issue
All volumes & issues
Special issues
Collections
Most read articles
Most cited articles

New content alerts
RSS

Your download is now in progress and you may close this window

Did you know that with a free Taylor & Francis Online account you can gain access to the following benefits?

Choose new content alerts to be informed about new research of interest to you
Easy remote access to your institution's subscriptions on any device, from any location
Save your searches and schedule alerts to send you new results
Export your search results into a .csv file to support your research

Have an account?
Login now Don't have an account?
Register for free

Login or register to access this feature

Have an account?
Login now Don't have an account?
Register for free

Choose new content alerts to be informed about new research of interest to you
Easy remote access to your institution's subscriptions on any device, from any location
Save your searches and schedule alerts to send you new results
Export your search results into a .csv file to support your research

Expert Opinion on Orphan Drugs, Volume 9, Issue 7-10 (2021)

Browse this journal

Current issue
List of issues
Special issues
Collections
Most read articles
Most cited articles

Sample our Medicine, Dentistry, Nursing & Allied Health journals, sign in here to start your FREE access for 14 days

Expert Opinion on Orphan Drugs, Volume 9, Issue 7-10 (2021)

See all volumes and issues

Vol 12, 2024 Vol 11, 2023 Vol 10, 2022 Volume 9, 2021 Vol 8, 2020 Vol 7, 2019 Vol 6, 2018 Vol 5, 2017 Vol 4, 2016 Vol 3, 2015 Vol 2, 2014 Vol 1, 2013

Select to download all citations or PDFs

Download citations Download PDFs Download issue

Browse by section (All)

Display order (Default)
Published online date
Page number
Section A-Z
Most read
Most cited

Drug Evaluation

Article

Lumasiran: expanding the treatment options for patients with primary hyperoxaluria type 1

Sally-Anne Hulton

Pages: 189-198

Published online: 25 Nov 2021

AbstractforLumasiran: expanding the treatment options for patients with primary hyperoxaluria type 1 | Full Text | References | PDF (1.7 MB) | EPUB

1964 Views
3 CrossRef citations
0Altmetric

Open Access

Article

An evaluation of onasemnogene abeparvovec for spinal muscular atrophy (SMN1)

Megan A. Waldrop, Anne M. Connolly & Jerry R. Mendell

Pages: 199-204

Published online: 25 Nov 2021

AbstractforAn evaluation of onasemnogene abeparvovec for spinal muscular atrophy (SMN1) | Full Text | References | PDF (886.5 KB) | EPUB

127 Views
0 CrossRef citations
0Altmetric

Review

Steroid alternatives for managing eosinophilic lung diseases

Quentin Delcros, Matthieu Groh, Mouhamad Nasser, Jean-Emmanuel Kahn & Vincent Cottin

Pages: 205-218

Published online: 03 Dec 2021

AbstractforSteroid alternatives for managing eosinophilic lung diseases | Full Text | References | PDF (2.4 MB) | EPUB

164 Views
3 CrossRef citations
0Altmetric

Systematic Review

Efficacy of sirolimus for treatment of autoimmune lymphoproliferative syndrome: a systematic review of open label clinical studies

Shweta Sharma, Md Sarfaraj Hussain, Nidhi.B. Agarwal, Dinesh Bhurani, Mohd Ashif Khan & Md Aejaz Ahmad Ansari

Pages: 219-226

Published online: 27 Aug 2021

AbstractforEfficacy of sirolimus for treatment of autoimmune lymphoproliferative syndrome: a systematic review of open label clinical studies | Full Text | References | PDF (580 KB) | EPUB

86 Views
1 CrossRef citations
0Altmetric

Explore articles

Latest
Open access
Most read
Most cited
Trending

Explore the most recently published articles

Current and emerging therapies for the treatment of leishmaniasis

Shyam Sundar et al.

Review Article | Published online: 1 Apr 2024

Open Access

The Orphan Drug Act and rare cancers: a retrospective analysis of oncologic orphan drug designations and associated approvals from 1983-2022

Abraham Viju Ipe et al.

Article | Published online: 26 Mar 2024

Open Access

Orphan drugs approved in Canada: health technology assessment, price negotiation, and government formulary listing

Nigel S B. Rawson et al.

Article | Published online: 13 Feb 2024

Open Access

Overview of genetic testing in Prader-Willi syndrome

Ying Gao et al.

Review Article | Published online: 28 Sep 2023

Open Access

Download citations

Choose format

RIS (ProCit, Reference Manager)
BibTeX
RefWorks Direct Export

Download citations

Expert Opinion on Orphan Drugs (Vol.9, Iss.7-10, 2021)

Access Rights

Only articles that you have access rights to view will be downloaded. The green tick (full access) and orange padlock (open access) icons indicate that you have full access.

Do you want to proceed?