Browse
We’re here to help

Find guidance on Author Services

Search
Browse
We’re here to help

Find guidance on Author Services

Home
All Journals
Expert Opinion on Orphan Drugs
List of Issues
Volume 3, Issue 11

Expert Opinion on Orphan Drugs

Search in:

Advanced search Citation search

Citation search

Ready to submit?
Start a new submission or continue a submission in progress
Go to submission site
Instructions for authors
Editorial policies
Editing services site

Journal metrics
Aims & scope
Journal information
Editorial board
News & calls for papers
Advertising information

Current issue
All volumes & issues
Special issues
Collections
Most read articles
Most cited articles

New content alerts
RSS

Your download is now in progress and you may close this window

Did you know that with a free Taylor & Francis Online account you can gain access to the following benefits?

Choose new content alerts to be informed about new research of interest to you
Easy remote access to your institution's subscriptions on any device, from any location
Save your searches and schedule alerts to send you new results
Export your search results into a .csv file to support your research

Have an account?
Login now Don't have an account?
Register for free

Login or register to access this feature

Have an account?
Login now Don't have an account?
Register for free

Choose new content alerts to be informed about new research of interest to you
Easy remote access to your institution's subscriptions on any device, from any location
Save your searches and schedule alerts to send you new results
Export your search results into a .csv file to support your research

Expert Opinion on Orphan Drugs, Volume 3, Issue 11 (2015)

Browse this journal

Current issue
List of issues
Special issues
Collections
Most read articles
Most cited articles

Sample our Bioscience journals, sign in here to start your access, Latest two full volumes FREE to you for 14 days

Expert Opinion on Orphan Drugs, Volume 3, Issue 11 (2015)

See all volumes and issues

Vol 12, 2024 Vol 11, 2023 Vol 10, 2022 Vol 9, 2021 Vol 8, 2020 Vol 7, 2019 Vol 6, 2018 Vol 5, 2017 Vol 4, 2016 Volume 3, 2015 Vol 2, 2014 Vol 1, 2013

Select to download all citations or PDFs

Download citations Download PDFs Download issue

Browse by section (All)

Display order (Default)
Published online date
Page number
Section A-Z
Most read
Most cited

Reviews

Prospective therapies for mucopolysaccharidoses

Anna Tylki-Szymańska MD PhD & Agnieszka Jurecka MD PhD

Pages: 1241-1253

Published online: 13 Nov 2015

AbstractforProspective therapies for mucopolysaccharidoses | Full Text | References | PDF (491 KB)

100 Views
0 CrossRef citations
0Altmetric

Gene therapy for Duchenne muscular dystrophy

Julian Ramos (Senior Fellow) PhD & Jeffrey S Chamberlain (Professor) PhD

Pages: 1255-1266

Published online: 06 Oct 2015

AbstractforGene therapy for Duchenne muscular dystrophy | Full Text | References | PDF (838.7 KB)

496 Views
37 CrossRef citations
0Altmetric

Treating hepatitis C in patients with hemoglobinopathies

Roberta D’Ambrosio, Erika Poggiali & Maria Domenica Cappellini

Pages: 1267-1278

Published online: 22 Sep 2015

AbstractforTreating hepatitis C in patients with hemoglobinopathies | Full Text | References | PDF (321.9 KB)

32 Views
0 CrossRef citations
0Altmetric

Enzyme replacement therapy for treating mucopolysaccharidosis type IVA (Morquio A syndrome): effect and limitations

Shunji Tomatsu (Professor and Director) MD PhD, Kazuki Sawamoto, Tsutomu Shimada, Michael B Bober, Francyne Kubaski, Eriko Yasuda, Robert W Mason, Shaukat Khan, Carlos J Alméciga-Díaz, Luis A Barrera, William G Mackenzie & Tadao Orii

Pages: 1279-1290

Published online: 29 Oct 2015

AbstractforEnzyme replacement therapy for treating mucopolysaccharidosis type IVA (Morquio A syndrome): effect and limitations | Full Text | References | PDF (264.6 KB)

205 Views
43 CrossRef citations
0Altmetric

Current and future treatment of infantile spasms

Svetlana Gataullina & Olivier Dulac

Pages: 1291-1297

Published online: 11 Sep 2015

AbstractforCurrent and future treatment of infantile spasms | Full Text | References | PDF (257.3 KB)

79 Views
0 CrossRef citations
0Altmetric

Childhood medulloblastoma: current and future treatment strategies

Tammy Hennika (Pediatric Neuro-Oncology Fellow) MD & Sridharan Gururangan (Professor of Pediatrics (with Tenure) and Associate Professor of Surgery, Director) FRCP

Pages: 1299-1317

Published online: 12 Sep 2015

AbstractforChildhood medulloblastoma: current and future treatment strategies | Full Text | References | PDF (1.4 MB)

102 Views
1 CrossRef citations
0Altmetric

Fabry disease: a review of current enzyme replacement strategies

Atul Mehta (Professor)

Pages: 1319-1330

Published online: 22 Sep 2015

AbstractforFabry disease: a review of current enzyme replacement strategies | Full Text | References | PDF (429.4 KB)

175 Views
3 CrossRef citations
0Altmetric

Drug Evaluations

Evaluation of collagenase Clostridium histolyticum for the treatment of Peyronie’s disease

Russell P Libby, Faysal A Yafi, James Anaissie & Wayne JG Hellstrom

Pages: 1331-1338

Published online: 24 Sep 2015

AbstractforEvaluation of collagenase Clostridium histolyticum for the treatment of Peyronie’s disease | Full Text | References | PDF (371.9 KB)

34 Views
0 CrossRef citations
0Altmetric

Article

Dasatinib for acute lymphoblastic leukemia

Françoise Huguet

Pages: 1339-1356

Published online: 13 Nov 2015

AbstractforDasatinib for acute lymphoblastic leukemia | Full Text | References | PDF (325.8 KB)

47 Views
0 CrossRef citations
0Altmetric

Afatinib for the treatment of non-small cell lung cancer

Federica Biello (Medical doctor) , Claudia Maggioni (Medical doctor) , Erika Rijavec (Medical doctor, Oncologist) , Carlo Genova (Medical doctor, Oncologist) , Giulia Barletta (Medical doctor, Oncologist) , Elisa Gualco (Medical doctor) , Anna Truini (Biologist) , Simona Coco (Biologist) , Maria Giovanna Dal Bello (Biologist) , Irene Vanni, Angela Alama (Biologist) , Francesco Boccardo (Medical doctor) & Francesco Grossi (Medical doctor, Oncologist)

Pages: 1357-1364

Published online: 22 Sep 2015

AbstractforAfatinib for the treatment of non-small cell lung cancer | Full Text | References | PDF (295.5 KB)

87 Views
1 CrossRef citations
0Altmetric

Explore articles

Latest
Open access
Most read
Most cited
Trending

Explore the most recently published articles

Current and emerging therapies for the treatment of leishmaniasis

Shyam Sundar et al.

Review Article | Published online: 1 Apr 2024

Open Access

The Orphan Drug Act and rare cancers: a retrospective analysis of oncologic orphan drug designations and associated approvals from 1983-2022

Abraham Viju Ipe et al.

Article | Published online: 26 Mar 2024

Open Access

Orphan drugs approved in Canada: health technology assessment, price negotiation, and government formulary listing

Nigel S B. Rawson et al.

Article | Published online: 13 Feb 2024

Open Access

Overview of genetic testing in Prader-Willi syndrome

Ying Gao et al.

Review Article | Published online: 28 Sep 2023

Open Access

Download citations

Choose format

RIS (ProCit, Reference Manager)
BibTeX
RefWorks Direct Export

Download citations

Expert Opinion on Orphan Drugs (Vol.3, Iss.11, 2015)

Access Rights

Only articles that you have access rights to view will be downloaded. The green tick (full access) and orange padlock (open access) icons indicate that you have full access.

Do you want to proceed?