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Amyloid
The Journal of Protein Folding Disorders
Volume 13, 2006 - Issue 4
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Original

Orally administered diflunisal stabilizes transthyretin against dissociation required for amyloidogenesis

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Pages 236-249 | Published online: 06 Jul 2009

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Read on this site (27)

Wenbing Zhang, Jian Ding, Wenhai Wang, Duo Wang, Yinping Pan & Dexin Xu. (2023) Status and Future Directions of Therapeutics and Prognosis of Cardiac Amyloidosis. Therapeutics and Clinical Risk Management 19, pages 581-597.
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Felix J. Tsai, Luke T. Nelson, Gabriel M. Kline, Marcus Jäger, John L. Berk, Yoshiki Sekijima, Evan T. Powers & Jeffery W. Kelly. (2023) Characterising diflunisal as a transthyretin kinetic stabilizer at relevant concentrations in human plasma using subunit exchange. Amyloid 30:2, pages 220-224.
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David A. Tess, Tristan S. Maurer, Zhenhong Li, Christine Bulawa, James Fleming & Amy T. Moody. (2023) Relationship of binding-site occupancy, transthyretin stabilisation and disease modification in patients with tafamidis-treated transthyretin amyloid cardiomyopathy. Amyloid 30:2, pages 208-219.
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Cecília Monteiro, Jaleh S. Mesgarzadeh, João Anselmo, Joana Fernandes, Marta Novais, Carla Rodrigues, David L. Powers, Evan T. Powers, Teresa Coelho & Jeffery W. Kelly. (2023) Tafamidis polyneuropathy amelioration requires modest increases in transthyretin stability even though increases in plasma native TTR and decreases in non-native TTR do not predict response. Amyloid 30:1, pages 81-95.
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Yusuke Takahashi, Nobuhiko Ohashi, Ken Takasone, Tsuneaki Yoshinaga, Masahide Yazaki, Michael Roberts, Paul F. Glidden & Yoshiki Sekijima. (2022) CSF/plasma levels, transthyretin stabilisation and safety of multiple doses of tolcapone in subjects with hereditary ATTR amyloidosis. Amyloid 29:3, pages 190-196.
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Arianna Burton, Adam Castaño, Marianna Bruno, Steve Riley, Jennifer Schumacher, Marla B Sultan, Sandi See Tai, Daniel P Judge, Jignesh K Patel & Jeffery W Kelly. (2021) Drug Discovery and Development in Rare Diseases: Taking a Closer Look at the Tafamidis Story. Drug Design, Development and Therapy 15, pages 1225-1243.
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Jeffery Kelly & Evan Powers. (2021) Response. Amyloid 28:2, pages 140-141.
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R. Spoladore, G. Falasconi, M. Marcatti, S. Di Maio, G. Fiore, M. Slavich, A. Margonato, A. Turco & G. Fragasso. (2021) Advances in pharmacotherapy for cardiac amyloidosis. Expert Opinion on Pharmacotherapy 22:4, pages 469-481.
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Luke T. Nelson, Ryan J. Paxman, Jin Xu, Bill Webb, Evan T. Powers & Jeffery W. Kelly. (2021) Blinded potency comparison of transthyretin kinetic stabilisers by subunit exchange in human plasma. Amyloid 28:1, pages 24-29.
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Xiaohua Guo, Zhaowen Liu, Yizhou Zheng, Yamei Li, Linfu Li, Hai Liu, Zhixi Chen & Longhuo Wu. (2020) Review on the Structures and Activities of Transthyretin Amyloidogenesis Inhibitors. Drug Design, Development and Therapy 14, pages 1057-1081.
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Veena Mathew & Annabel K Wang. (2019) Inotersen: new promise for the treatment of hereditary transthyretin amyloidosis. Drug Design, Development and Therapy 13, pages 1515-1525.
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Prakash Harikrishnan, Srikanth Yandrapalli, Wilbert S. Aronow, Gregg M. Lanier & Diwakar Jain. (2019) Novel drug therapies for cardiac amyloidosis. Expert Opinion on Investigational Drugs 28:6, pages 497-499.
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Asad Ikram, Joseph P. Donnelly, Brett W. Sperry, Christy Samaras, Jason Valent & Mazen Hanna. (2018) Diflunisal tolerability in transthyretin cardiac amyloidosis: a single center’s experience. Amyloid 25:3, pages 197-202.
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Hirofumi Jono & Yukio Ando. (2017) Towards targets and treatments in transthyretin amyloidosis. Expert Opinion on Orphan Drugs 5:9, pages 691-699.
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Sayaka Matsumoto, Mitsuharu Ueda, Taro Yamashita, Tomoko Amano, Yohei Misumi, Masayoshi Tasaki, Teruaki Masuda, Mayumi Mizukami, Hirokazu Furuya & Yukio Ando. (2017) A late-onset case of hereditary transthyretin amyloidosis with a novel compound heterozygous mutation. Amyloid 24:sup1, pages 97-98.
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Lixia Qiang, Yanxia Guan, Xiangshun Li, Li Liu, Yanshuang Mu, Aki Sugano, Yutaka Takaoka, Toshiyuki Sakaeda, Bruno P. Imbimbo, Ken-Ichi Yamamura, Shoude Jin & Zhenghua Li. (2017) CSP-1103 (CHF5074) stabilizes human transthyretin in healthy human subjects. Amyloid 24:1, pages 42-51.
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Lidia Ciccone, Susanna Nencetti, Armando Rossello, Livia Tepshi, Enrico A. Stura & Elisabetta Orlandini. (2016) X-ray crystal structure and activity of fluorenyl-based compounds as transthyretin fibrillogenesis inhibitors. Journal of Enzyme Inhibition and Medicinal Chemistry 31:5, pages 824-833.
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Philip N. Hawkins, Yukio Ando, Angela Dispenzeri, Alejandra Gonzalez-Duarte, David Adams & Ole B. Suhr. (2015) Evolving landscape in the management of transthyretin amyloidosis. Annals of Medicine 47:8, pages 625-638.
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Giovanni Palladini, Paolo Milani & Giampaolo Merlini. (2015) Novel strategies for the diagnosis and treatment of cardiac amyloidosis. Expert Review of Cardiovascular Therapy 13:11, pages 1195-1211.
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Yoshiki Sekijima, Kana Tojo, Hiroshi Morita, Jun Koyama & Shu-ichi Ikeda. (2015) Safety and efficacy of long-term diflunisal administration in hereditary transthyretin (ATTR) amyloidosis. Amyloid 22:2, pages 79-83.
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Laura Obici & Giampaolo Merlini. (2014) An overview of drugs currently under investigation for the treatment of transthyretin-related hereditary amyloidosis. Expert Opinion on Investigational Drugs 23:9, pages 1239-1251.
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Michitaka Nakagawa, Yoshiki Sekijima, Kana Tojo & Shu-Ichi Ikeda. (2013) High prevalence of ATTR amyloidosis in endomyocardial biopsy-proven cardiac amyloidosis patients. Amyloid 20:2, pages 138-140.
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John L. Berk, Ole B. Suhr, Yoshiki Sekijima, Taro Yamashita, Michael Heneghan, Steven R. Zeldenrust, Yukio Ando, Shu-ichi Ikeda, Peter Gorevic, Giampaolo Merlini, Jeffrey W. Kelly, Martha Skinner, Alice B. Bisbee, Peter J. Dyck & Laura Obici. (2012) The Diflunisal Trial: Study accrual and drug tolerance. Amyloid 19:sup1, pages 37-38.
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Adam Castaño, Sabahat Bokhari, Thomas H. Brannagan$suffix/text()$suffix/text(), Julia Wynn & Mathew S. Maurer. (2012) Technetium pyrophosphate myocardial uptake and peripheral neuropathy in a rare variant of familial transthyretin (TTR) amyloidosis (Ser23Asn): a case report and literature review. Amyloid 19:1, pages 41-46.
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J. L. Berk, P. J. Dyck, L. Obici, S. R. Zeldenrust, Y. Sekijima, T. Yamashita, Y. Ando, S.-I. Ikeda, P. Gorevic, G. Merlini, J. W. Kelly, M. Skinner, A. B. Bisbee & O. B. Suhr. (2011) The diflunisal trial: update on study drug tolerance and disease progression. Amyloid 18:sup1, pages 196-197.
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Chloe M. Mak, Yok-Lam Kwong, Ching-Wan Lam, See-Ching Chan, Chung-Mau Lo, Sheung-Tak Fan, Chee-My Chang, Yuk-Kwong Lau, Lok-Sun U & Sidney Tam. (2007) Identification of a novel TTR Gly67Glu mutant and the first case series of familial transthyretin amyloidosis in Hong Kong Chinese. Amyloid 14:4, pages 293-297.
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